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NCT06462547 · ClinicalTrials.gov registry record · Phase 2

ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency

A Phase 2 study of Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency and Pseudoxanthoma Elasticum, sponsored by Inozyme Pharma.

Recruiting
Registry status
Phase 2
Development phase
200
Enrollment target
5
Study locations

NCT06462547 is a Phase 2 study of Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency and Pseudoxanthoma Elasticum that is actively recruiting participants, run by Inozyme Pharma. The registered enrollment target is 200 participants, above the 17-participant average among 3 other Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency trials with a reported enrollment target (1076% higher). The trial reports 5 study locations across 3 states.

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The verdict

NCT06462547, a Phase 2 study of Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency and Pseudoxanthoma Elasticum, is actively recruiting participants, sponsored by Inozyme Pharma.

RECRUITING
Registry status
Phase 2
Development phase
200 participants
Enrollment target
5
Study locations

Study Summary

The purpose of this study (Study INZ701-304 \[ADAPT\]) is to assess the long-term safety of INZ-701 in patients with ENPP1 Deficiency or ABCC6 Deficiency who have received INZ-701 in an existing clinical study and choose to continue dosing for the potential treatment of their condition.

Interventions

  • DRUG INZ-701

Study Locations (5)

Other

  • Necker-Enfants Malades Hospital - Paris
  • Universitätsklinikum Hamburg-Eppendorf (UKE) - Hamburg
  • VCTC - Oxford

Minnesota

  • Mayo Clinic - Rochester

New Jersey

  • Clinilabs Drug Development Corporation - Eatontown

Trial Details

FieldValue
Enrollment Target 200 participants
Start Date 2024-06-19
Est. Completion 2030-12
Phase Phase 2

Sponsor

Inozyme Pharma

9 total trials

What the Registry Record Tells You About NCT06462547

The ClinicalTrials.gov registry entry for NCT06462547 describes a study currently listed as recruiting, categorized as Phase 2. The registered enrollment target is 200 participants, a figure that helps gauge the scale of data the investigators plan to collect, above the 17-participant average among 3 other Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency trials with a reported enrollment target (1076% higher). The listed sponsor is Inozyme Pharma, which has 9 total studies on file at ClinicalTrials.gov.

The record links to 5 conditions, with Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency appearing as the primary indexed condition, and to 1 intervention - of which INZ-701 is the first listed.

NCT06462547 reports 5 study locations spanning 3 distinct geographic areas - top geographies include Other, Minnesota, New Jersey.

Frequently Asked Questions

What is clinical trial NCT06462547 about?

NCT06462547 is a clinical study titled "ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency". The purpose of this study (Study INZ701-304 \[ADAPT\]) is to assess the long-term safety of INZ-701 in patients with ENPP1 Deficiency or ABCC6 Deficiency who have received INZ-701 in an existing clinical study and choose to continue dosing for the potential treatment of their condition.

What is the current status of trial NCT06462547?

This trial is currently recruiting. It is a Phase 2 study. The enrollment target is 200 participants. The study started on 2024-06-19. Estimated completion is 2030-12.

What conditions does trial NCT06462547 study?

This clinical trial studies the following conditions: Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency, Pseudoxanthoma Elasticum, Arterial Calcification, Autosomal Recessive Hypophosphatemic Rickets Type 2, Gene Mutations.

What interventions are being tested in trial NCT06462547?

The interventions under investigation include: INZ-701 (DRUG).

Who is sponsoring clinical trial NCT06462547?

This trial is sponsored by Inozyme Pharma, which has 9 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT06462547 being conducted?

This trial has 5 study locations across Minnesota, New Jersey. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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