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NCT05468359 · ClinicalTrials.gov registry record · Phase 1

Safety and Efficacy of Cyclophosphamide, Sorafenib, Bevacizumab, and Atezolizumab in Pediatric Solid Tumor Patients

A Phase 1 study of Hepatocellular Carcinoma and Pediatric Cancer, sponsored by St. Jude Children's Research Hospital.

Recruiting
Registry status
Phase 1
Development phase
64
Enrollment target
2
Study locations

NCT05468359 is a Phase 1 study of Hepatocellular Carcinoma and Pediatric Cancer that is actively recruiting participants, run by St. Jude Children's Research Hospital. The registered enrollment target is 64 participants, below the 257-participant average among 145 other Hepatocellular Carcinoma trials with a reported enrollment target (75% lower). The trial reports 2 study locations across 1 state.

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The verdict

NCT05468359, a Phase 1 study of Hepatocellular Carcinoma and Pediatric Cancer, is actively recruiting participants, sponsored by St. Jude Children's Research Hospital.

RECRUITING
Registry status
Phase 1
Development phase
64 participants
Enrollment target
2
Study locations

Study Summary

This is a phase I/II study to evaluate the safety of combining intravenous (IV) atezolizumab and bevacizumab every three weeks, with daily oral cyclophosphamide and pharmacokinetic (PK)-guided sorafenib in children and adolescent and young adults (AYA) with relapsed or refractory solid malignancies (Part 1), and then evaluate the response rate of this combination in children, AYA with relapsed or refractory fibrolamellar carcinoma (FLC) and other rare solid malignancies (Part 2). Primary Objectives Part 1 * To establish the safety associated with the administration of the combination of cyclophosphamide, PK-guided sorafenib, bevacizumab and atezolizumab in children and AYA with relapsed or refractory solid tumors * To determine if sorafenib systemic exposure can be successfully targeted to an AUC between 20 and 55 hr·µg/mL by Day 21 of cycle 1 in 60% of evaluable patients, when given in combination with cyclophosphamide, bevacizumab, and atezolizumab in children and AYA with relapsed or refractory solid tumors Part 2 * To evaluate the response rate (CR+PR) of the combination of cyclophosphamide, PK-guided sorafenib, bevacizumab and atezolizumab in children and AYA with relapsed or refractory FLC following two cycles of therapy * To determine if the use of PK-guided sorafenib dosing to maintain a systemic exposure between 20 and 55 reduces the interpatient pharmacokinetic variability of sorafenib and the incidence of sorafenib- induced skin toxicities in children and AYA with relapsed or refractory FLC and other rare solid tumors Parts 1 \& 2 * To determine if the combination of cyclophosphamide, PK-guided sorafenib and atezolizumab will result in increased intratumoral T-cell infiltration of CD8+C45RO+ cells between baseline and following two courses of therapy in pediatric children and AYA with relapsed or refractory solid tumors following two cycles of therapy * To characterize the pharmacokinetics of atezolizumab in combination with cyclophosphamide, PK-gui

Interventions

  • DRUG Cyclophosphamide
  • DRUG Bevacizumab
  • DRUG Atezolizumab
  • DRUG Sorafenib

Study Locations (2)

Tennessee

  • Methodist Le Bonheur Healthcare - Germantown
  • St. Jude Children's Research Hospital - Memphis

Trial Details

FieldValue
Enrollment Target 64 participants
Start Date 2022-11-07
Est. Completion 2037-06
Phase Phase 1

What the Registry Record Tells You About NCT05468359

The ClinicalTrials.gov registry entry for NCT05468359 describes a study currently listed as recruiting, categorized as Phase 1. The registered enrollment target is 64 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 257-participant average among 145 other Hepatocellular Carcinoma trials with a reported enrollment target (75% lower). The listed sponsor is St. Jude Children's Research Hospital, which has 410 total studies on file at ClinicalTrials.gov.

The record links to 6 conditions, with Hepatocellular Carcinoma appearing as the primary indexed condition, and to 4 interventions - of which Cyclophosphamide is the first listed.

NCT05468359 reports 2 study locations spanning 1 distinct geographic area - top geographies include Tennessee.

Frequently Asked Questions

What is clinical trial NCT05468359 about?

NCT05468359 is a clinical study titled "Safety and Efficacy of Cyclophosphamide, Sorafenib, Bevacizumab, and Atezolizumab in Pediatric Solid Tumor Patients". This is a phase I/II study to evaluate the safety of combining intravenous (IV) atezolizumab and bevacizumab every three weeks, with daily oral cyclophosphamide and pharmacokinetic (PK)-guided sorafenib in children and adolescent and young adults (AYA) with relapsed or refractory solid malignancies ...

What is the current status of trial NCT05468359?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 64 participants. The study started on 2022-11-07. Estimated completion is 2037-06.

What conditions does trial NCT05468359 study?

This clinical trial studies the following conditions: Hepatocellular Carcinoma, Pediatric Cancer, Pediatric Solid Tumor, Malignant Solid Tumor, Fibrolamellar Carcinoma.

What interventions are being tested in trial NCT05468359?

The interventions under investigation include: Cyclophosphamide (DRUG), Bevacizumab (DRUG), Atezolizumab (DRUG), Sorafenib (DRUG).

Who is sponsoring clinical trial NCT05468359?

This trial is sponsored by St. Jude Children's Research Hospital, which has 410 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05468359 being conducted?

This trial has 2 study locations across Tennessee. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.