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NCT04954001 · ClinicalTrials.gov registry record · Phase 1

Study to Evaluate the Safety, Tolerability, PK Characteristics and Anti-tumor Activity of FCN-159 in Adult and Pediatric Participants With Neurofibromatosis Type 1

A Phase 1 study of Neurofibromatosis 1 and Plexiform Neurofibroma, sponsored by Shanghai Fosun Pharmaceutical Industrial Development Co..

Active
Registry status
Phase 1
Development phase
160
Enrollment target
14
Study locations

NCT04954001: Active Phase 1 study of Neurofibromatosis 1 and Plexiform Neurofibroma, sponsored by Shanghai Fosun Pharmaceutical Industrial Development Co..

NCT04954001 is a Phase 1 study of Neurofibromatosis 1 and Plexiform Neurofibroma that is active but no longer recruiting, run by Shanghai Fosun Pharmaceutical Industrial Development Co.. The registered enrollment target is 160 participants, below the 1,029-participant average among 24 other Neurofibromatosis 1 trials with a reported enrollment target (84% lower). The trial reports 14 study locations across 5 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04954001, a Phase 1 study of Neurofibromatosis 1 and Plexiform Neurofibroma, is active but no longer recruiting, sponsored by Shanghai Fosun Pharmaceutical Industrial Development Co..

ACTIVE NOT RECRUITING
Registry status
Phase 1
Development phase
160 participants
Enrollment target
14
Study locations

Study Summary

FCN-159 is a highly active MEK1/2 inhibitor that was designed, synthesized and screened on the basis of the structure of trametinib. FCN-159 is an orally available and highly potent selective inhibitor of MEK1/2, which is expected to be a targeted therapy for the treatment of advanced solid tumors and neurofibromatosis type 1.

Interventions

  • DRUG FCN-159

Study Locations (14)

Other

  • Research Site - Beijing
  • Research Site - Guangzhou
  • Research Site - Hangzhou
  • Research Site - Shanghai
  • Research Site - Shijiazhuang
  • Research Site - Wuhan
  • Hospital Universitario Vall d'Hebron - Barcelona
  • Hospital Universitario 12 de Octubre - Madrid
  • Hospital Universitario La Paz - Madrid

Florida

  • Principal Investigator Hans - Gainesville
  • John Hopkins All Children Hospital - St. Petersburg

California

  • Children's Hospital Los Angeles - Los Angeles

Michigan

  • Henry Ford Health System - Detroit

South Carolina

  • Medical University of South Carolina - Hollings Cancer Center - PPDS - Charleston

Trial Details

FieldValue
Enrollment Target 160 participants
Start Date 2021-03-26
Est. Completion 2025-03-30
Phase Phase 1

What the registry record for NCT04954001 still lists

NCT04954001 is an interventional study that assigns participants to a tested intervention. The registered 160 participants enrollment target is mid-sized for trials with a published cap, below the 1,029-participant average among 24 other Neurofibromatosis 1 trials with a reported enrollment target (84% lower).

The record links to 3 conditions, with Neurofibromatosis 1 appearing as the primary indexed condition, and to 1 intervention - of which FCN-159 is the first listed.

NCT04954001 lists 14 locations in 5 states (Other, Florida, California).

Frequently Asked Questions

What is clinical trial NCT04954001 about?

NCT04954001 is a clinical study titled "Study to Evaluate the Safety, Tolerability, PK Characteristics and Anti-tumor Activity of FCN-159 in Adult and Pediatric Participants With Neurofibromatosis Type 1". FCN-159 is a highly active MEK1/2 inhibitor that was designed, synthesized and screened on the basis of the structure of trametinib. FCN-159 is an orally available and highly potent selective inhibitor of MEK1/2, which is expected to be a targeted therapy for the treatment of advanced solid tumors a...

What is the current status of trial NCT04954001?

This trial is currently active not recruiting. It is a Phase 1 study. The enrollment target is 160 participants. The study started on 2021-03-26. Estimated completion is 2025-03-30.

What conditions does trial NCT04954001 study?

This clinical trial studies the following conditions: Neurofibromatosis 1, Plexiform Neurofibroma, NF1.

What interventions are being tested in trial NCT04954001?

The interventions under investigation include: FCN-159 (DRUG).

Who is sponsoring clinical trial NCT04954001?

This trial is sponsored by Shanghai Fosun Pharmaceutical Industrial Development Co., which has 2 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04954001 being conducted?

This trial has 14 study locations across California, Florida, Michigan, South Carolina. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Neurofibromatosis 1

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT04954001's enrollment target sits among peer trials

160 10th of 24 higher than 15 of 24 other Neurofibromatosis 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Neurofibromatosis 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT04954001, the US trial registry maintained by the National Library of Medicine. NCT04954001 (mid enrollment · multi site footprint · active not recruiting) retrieved and formatted by PlainTrial, see methodology.