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NCT04639336 · ClinicalTrials.gov registry record
Cognitive and Neurological Pathologies in Pompe Disease
A clinical trial of Pompe Disease, sponsored by Duke University.
- Recruiting
- Registry status
- 45
- Enrollment target
- 1
- Study location
NCT04639336 is a study of Pompe Disease that is actively recruiting participants, run by Duke University. The registered enrollment target is 45 participants, below the 229-participant average among 14 other Pompe Disease trials with a reported enrollment target (80% lower). The trial reports 1 study location across 1 state.
The verdict
NCT04639336, a study of Pompe Disease, is actively recruiting participants, sponsored by Duke University.
- RECRUITING
- Registry status
- 45 participants
- Enrollment target
- 1
- Study location
Study Summary
The purpose of this study is to better understand the long-term health effects of Pompe disease and to determine if there are any abnormal changes in the brain and peripheral nerves. Additionally, the investigators will study the relationship between the abnormal changes in brain, nervous system findings, and developmental outcomes. The investigators will collect clinical information from clinic visits as well as assessments such as neuroimaging (magnetic resonance imaging (MRI), magnetic resonance spectroscopy (MRS), and diffusion tensor imaging (DTI)), cognition, academic skills, speech and language function, physical therapy and quantitative muscle ultrasound. Subjects will be in this study for at least 3 years and up to 6 years.
Conditions Studied
Study Locations (1)
North Carolina
- Duke University Medical Center - Durham
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 45 participants |
| Start Date | 2016-08-03 |
| Est. Completion | 2029-03 |
Interested in This Trial?
Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT04639336
The ClinicalTrials.gov registry entry for NCT04639336 describes a study currently listed as recruiting, categorized as an unspecified phase. The registered enrollment target is 45 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 229-participant average among 14 other Pompe Disease trials with a reported enrollment target (80% lower). The listed sponsor is Duke University, which has 1,725 total studies on file at ClinicalTrials.gov.
The record links to 1 condition, with Pompe Disease appearing as the primary indexed condition, and to 0 interventions.
NCT04639336 reports 1 study location spanning 1 distinct geographic area - top geographies include North Carolina.
Frequently Asked Questions
What is clinical trial NCT04639336 about?
NCT04639336 is a clinical study titled "Cognitive and Neurological Pathologies in Pompe Disease". The purpose of this study is to better understand the long-term health effects of Pompe disease and to determine if there are any abnormal changes in the brain and peripheral nerves. Additionally, the investigators will study the relationship between the abnormal changes in brain, nervous system fin...
What is the current status of trial NCT04639336?
This trial is currently recruiting. The enrollment target is 45 participants. The study started on 2016-08-03. Estimated completion is 2029-03.
What conditions does trial NCT04639336 study?
This clinical trial studies the following conditions: Pompe Disease.
Who is sponsoring clinical trial NCT04639336?
This trial is sponsored by Duke University, which has 1,725 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04639336 being conducted?
This trial has 1 study location across North Carolina. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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Read our methodology - how this data is sourced, computed, and verified.
Related
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