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NCT04598477 · ClinicalTrials.gov registry record · Phase 3

A Study to Assess the Long-term Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod PH20 SC in Adults With Pemphigus (Vulgaris or Foliaceus)

A Phase 3 study, sponsored by argenx.

Terminated
Registry status
Phase 3
Development phase
183
Enrollment target

NCT04598477: Clinical Trial Phase 3 study, sponsored by argenx.

NCT04598477 is a Phase 3 study that was terminated before completion, run by argenx. The registered enrollment target is 183 participants, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (76% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04598477, a Phase 3 study, was terminated before completion, sponsored by argenx.

TERMINATED
Registry status
Phase 3
Development phase
183 participants
Enrollment target

Study Summary

This was a prospective, multicenter, open label extension (OLE) trial on the efficacy, safety, patient outcome measures, tolerability, immunogenicity, PK and PD of efgartigimod PH20 SC in adult PV or PF participants, who participated in antecedent trial ARGX-113-1904. This trial provided extension of efgartigimod PH20 SC treatment and retreatment options for participants who had been randomized to efgartigimod PH20 SC treatment arm in the trial ARGX-113-1904, and first treatment of efgartigimod PH20 SC and retreatment options for participants who had been randomized to the placebo arm in trial ARGX-113-1904. The participants could also receive concomitant prednisone therapy. Investigators could increase or decrease the prednisone dose based on protocol-specified criteria. Trial ARGX-113-1905 evaluated the ability to (further) taper prednisone therapy and achieve Clinical Remission (CR) off therapy (CRoff), the ability to achieve CR and CR on minimal therapy (CRmin) for participants who had not yet achieved CR or CRmin, and the ability to treat flare; it also assessed patient outcome measures and the safety, PD, PK and immunogenicity of efgartigimod PH20 SC over the duration of trial. Study duration: Up to 60 weeks for participants who receive IMP administration up to 52 weeks and with a follow-up period of 8 weeks after the last IMP administration

Primary Outcome

Incidence rates were calculated as 100 × n/PYFU. PYFU=participant-years of follow-up. The safety data sets includes participants with pemphigus vulgaris (PV) and pemphigus foliaceus (PF).

Interventions

  • DRUG prednisone
  • BIOLOGICAL efgartigimod PH20 SC

Trial Details

FieldValue
Enrollment Target 183 participants
Start Date 2021-07-15
Est. Completion 2024-03-25
Phase Phase 3
argenx

49 total trials

Why NCT04598477 stopped before completion

NCT04598477 is an interventional study that assigns participants to a tested intervention. The registered 183 participants enrollment target is mid-sized for trials with a published cap, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (76% lower).

The record links to 0 conditions, and to 2 interventions - of which prednisone is the first listed.

NCT04598477 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT04598477 about?

NCT04598477 is a clinical study titled "A Study to Assess the Long-term Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod PH20 SC in Adults With Pemphigus (Vulgaris or Foliaceus)". This was a prospective, multicenter, open label extension (OLE) trial on the efficacy, safety, patient outcome measures, tolerability, immunogenicity, PK and PD of efgartigimod PH20 SC in adult PV or PF participants, who participated in antecedent trial ARGX-113-1904. This trial provided extension o...

What is the current status of trial NCT04598477?

This trial is currently terminated. It is a Phase 3 study. The enrollment target is 183 participants. The study started on 2021-07-15. Estimated completion is 2024-03-25.

What interventions are being tested in trial NCT04598477?

The interventions under investigation include: prednisone (DRUG), efgartigimod PH20 SC (BIOLOGICAL).

Who is sponsoring clinical trial NCT04598477?

This trial is sponsored by argenx, which has 49 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT04598477's enrollment target sits among peer trials

183 1420th of 2000 higher than 580 of 2,000 other Phase 3 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 3 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT04598477, the US trial registry maintained by the National Library of Medicine. NCT04598477 (mid enrollment · none site footprint · terminated) retrieved and formatted by PlainTrial, see methodology.