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NCT04273243 · ClinicalTrials.gov registry record
Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
A clinical trial of Batten Disease and CLN6, sponsored by Emily de los Reyes.
- Active
- Registry status
- 10
- Enrollment target
- 1
- Study location
NCT04273243 is a study of Batten Disease and CLN6 that is active but no longer recruiting, run by Emily de los Reyes. The registered enrollment target is 10 participants, below the 2,829-participant average among 11 other Batten Disease trials with a reported enrollment target (100% lower). The trial reports 1 study location across 1 state.
The verdict
NCT04273243, a study of Batten Disease and CLN6, is active but no longer recruiting, sponsored by Emily de los Reyes.
- ACTIVE NOT RECRUITING
- Registry status
- 10 participants
- Enrollment target
- 1
- Study location
Study Summary
This is a long-term safety and efficacy study in subjects with CLN6 Batten disease who previously received a single intrathecal administration of AT-GTX-501.
Conditions Studied
Interventions
- GENETIC AT-GTX-501
Study Locations (1)
Ohio
- Nationwide Children's Hosptial - Columbus
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 10 participants |
| Start Date | 2020-01-24 |
| Est. Completion | 2027-12 |
Interested in This Trial?
Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT04273243
The ClinicalTrials.gov registry entry for NCT04273243 describes a study currently listed as active not recruiting, categorized as an unspecified phase. The registered enrollment target is 10 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 2,829-participant average among 11 other Batten Disease trials with a reported enrollment target (100% lower). The listed sponsor is Emily de los Reyes, which has 4 total studies on file at ClinicalTrials.gov.
The record links to 2 conditions, with Batten Disease appearing as the primary indexed condition, and to 1 intervention - of which AT-GTX-501 is the first listed.
NCT04273243 reports 1 study location spanning 1 distinct geographic area - top geographies include Ohio.
Frequently Asked Questions
What is clinical trial NCT04273243 about?
NCT04273243 is a clinical study titled "Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer". This is a long-term safety and efficacy study in subjects with CLN6 Batten disease who previously received a single intrathecal administration of AT-GTX-501.
What is the current status of trial NCT04273243?
This trial is currently active not recruiting. The enrollment target is 10 participants. The study started on 2020-01-24. Estimated completion is 2027-12.
What conditions does trial NCT04273243 study?
This clinical trial studies the following conditions: Batten Disease, CLN6.
What interventions are being tested in trial NCT04273243?
The interventions under investigation include: AT-GTX-501 (GENETIC).
Who is sponsoring clinical trial NCT04273243?
This trial is sponsored by Emily de los Reyes, which has 4 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04273243 being conducted?
This trial has 1 study location across Ohio. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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Read our methodology - how this data is sourced, computed, and verified.
Related
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.