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NCT04257929 · ClinicalTrials.gov registry record · Phase 2

A Phase 2 Study to Evaluate the Safety and Efficacy of Pitolisant in Patients With Prader-Willi Syndrome, Followed by an Open Label Extension

A Phase 2 study of Prader-Willi Syndrome, sponsored by Harmony Biosciences Management.

Active
Registry status
Phase 2
Development phase
65
Enrollment target
13
Study locations

NCT04257929 is a Phase 2 study of Prader-Willi Syndrome that is active but no longer recruiting, run by Harmony Biosciences Management. The registered enrollment target is 65 participants, roughly in line with the 67-participant average among 16 other Prader-Willi Syndrome trials with a reported enrollment target. The trial reports 13 study locations across 10 states.

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The verdict

NCT04257929, a Phase 2 study of Prader-Willi Syndrome, is active but no longer recruiting, sponsored by Harmony Biosciences Management.

ACTIVE NOT RECRUITING
Registry status
Phase 2
Development phase
65 participants
Enrollment target
13
Study locations

Study Summary

The primary objective of this study is to evaluate the safety and efficacy of pitolisant compared with placebo in treating excessive daytime sleepiness (EDS) in patients with Prader Willi syndrome (PWS) ages 6 to 65 years.

Conditions Studied

Interventions

  • DRUG Placebo oral tablet
  • DRUG Pitolisant oral tablets

Study Locations (13)

California

  • Rady Children's Hospital - San Diego - San Diego
  • Sleep Medicine Specialists of California - San Ramon
  • Santa Monica Clinical Trials - Santa Monica

Texas

  • Texas Children's Hospital/Baylor College of Medicine - Houston
  • Road Runner Research - San Antonio

Colorado

  • Children's Hospital Colorado - Aurora

Delaware

  • Nemours Alfred I duPont Hospital for Children - Wilmington

Florida

  • University of Florida College of Medicine - Gainesville

Illinois

  • Ann and Robert H Lurie Children's Hospital - Chicago

Maryland

  • Johns Hopkins School of Medicine - Baltimore

Nebraska

  • University of Nebraska Medical Center - Omaha

Trial Details

FieldValue
Enrollment Target 65 participants
Start Date 2020-12-09
Est. Completion 2028-09-07
Phase Phase 2

Sponsor

Harmony Biosciences Management

10 total trials

What the Registry Record Tells You About NCT04257929

The ClinicalTrials.gov registry entry for NCT04257929 describes a study currently listed as active not recruiting, categorized as Phase 2. The registered enrollment target is 65 participants, a figure that helps gauge the scale of data the investigators plan to collect, roughly in line with the 67-participant average among 16 other Prader-Willi Syndrome trials with a reported enrollment target. The listed sponsor is Harmony Biosciences Management, which has 10 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Prader-Willi Syndrome appearing as the primary indexed condition, and to 2 interventions - of which Placebo oral tablet is the first listed.

NCT04257929 reports 13 study locations spanning 10 distinct geographic areas - top geographies include California, Texas, Colorado.

Frequently Asked Questions

What is clinical trial NCT04257929 about?

NCT04257929 is a clinical study titled "A Phase 2 Study to Evaluate the Safety and Efficacy of Pitolisant in Patients With Prader-Willi Syndrome, Followed by an Open Label Extension". The primary objective of this study is to evaluate the safety and efficacy of pitolisant compared with placebo in treating excessive daytime sleepiness (EDS) in patients with Prader Willi syndrome (PWS) ages 6 to 65 years.

What is the current status of trial NCT04257929?

This trial is currently active not recruiting. It is a Phase 2 study. The enrollment target is 65 participants. The study started on 2020-12-09. Estimated completion is 2028-09-07.

What conditions does trial NCT04257929 study?

This clinical trial studies the following conditions: Prader-Willi Syndrome.

What interventions are being tested in trial NCT04257929?

The interventions under investigation include: Placebo oral tablet (DRUG), Pitolisant oral tablets (DRUG).

Who is sponsoring clinical trial NCT04257929?

This trial is sponsored by Harmony Biosciences Management, which has 10 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04257929 being conducted?

This trial has 13 study locations across California, Colorado, Delaware, Florida, Illinois. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Prader-Willi Syndrome

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.