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NCT03140527 · ClinicalTrials.gov registry record · Phase 1

Study Assessing the Safety, Tolerability, Pharmacokinetics, Food Effect, and Drug-Drug Interactions of PTI-801 in Healthy Volunteers, and Safety, Tolerability, and Pharmacokinetics of PTI-801 in Subjects With Cystic Fibrosis

A Phase 1 study of Cystic Fibrosis and Healthy Volunteer, sponsored by Proteostasis Therapeutics.

Completed
Registry status
Phase 1
Development phase
171
Enrollment target
20
Study locations

NCT03140527: Completed Phase 1 study of Cystic Fibrosis and Healthy Volunteer, sponsored by Proteostasis Therapeutics.

NCT03140527 is a Phase 1 study of Cystic Fibrosis and Healthy Volunteer that has completed, run by Proteostasis Therapeutics. The registered enrollment target is 171 participants, roughly in line with the 178-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target. The trial reports 20 study locations across 15 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT03140527, a Phase 1 study of Cystic Fibrosis and Healthy Volunteer, has completed, sponsored by Proteostasis Therapeutics.

COMPLETED
Registry status
Phase 1
Development phase
171 participants
Enrollment target
20
Study locations

Study Summary

This trial will consist of two parts: Part 1 and Part 2. Part 1 will enroll adult healthy volunteers (HV) into four treatment groups. The first group will enroll HV into a single ascending dose (SAD) treatment group consisting of three cohorts. The second group will enroll HV into a multiple ascending dose (MAD) treatment group consisting of three cohorts. The third group will enroll HV into a food effect (FE) treatment group consisting of one cohort. The fourth group will enroll HV into a drug-drug interactions (DDI) treatment group consisting of one cohort. Approximately 76 subjects will be enrolled in Part 1. Part 2 Cohorts 1 through 3 will enroll adult subjects with cystic fibrosis (CF) currently on stable ivacaftor/lumacaftor background therapy for a minimum of three months. Part 2 Cohorts 4 and Cohort 5 will enroll adult subjects with CF not currently receiving cystic fibrosis conductance regulator (CFTR) modulator therapy within 30 days prior to Day 1. Part 2 Cohort 6 will enroll adult subjects with cystic fibrosis on stable tezacaftor/ivacaftor background therapy. Approximately 104 subjects will be enrolled in Part 2.

Interventions

  • DRUG Placebo
  • DRUG PTI-808
  • DRUG PTI-801

Study Locations (20)

Florida

  • Central Florida Pulmonary Group - Altamonte Springs
  • University of Florida College of Medicine - Gainesville
  • University of Miami Health System - Miami

Illinois

  • Northwestern University Memorial Hospital - Chicago
  • OSF Saint Francis Medical Center - Peoria

Massachusetts

  • Massachusetts General Hospital - Boston
  • Boston Children's Hospital - Boston

New York

  • Columbia University Medical Center - New York
  • Mount Sinai Beth Israel - New York

Alabama

  • University of Alabama at Birmingham - Birmingham

Alaska

  • Providence Alaska Medical Center - Anchorage

California

  • Stanford University Medical Center - Stanford

Colorado

  • National Jewish Health - Denver

Trial Details

FieldValue
Enrollment Target 171 participants
Start Date 2017-04-10
Est. Completion 2020-02-27
Phase Phase 1
Proteostasis Therapeutics

5 total trials

What the finished NCT03140527 record still lists

NCT03140527 is an interventional study that assigns participants to a tested intervention. The registered 171 participants enrollment target is mid-sized for trials with a published cap, roughly in line with the 178-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target.

The record links to 2 conditions, with Cystic Fibrosis appearing as the primary indexed condition, and to 3 interventions - of which Placebo is the first listed.

NCT03140527 names 20 study sites across 15 states, led by Florida, Illinois, Massachusetts.

Frequently Asked Questions

What is clinical trial NCT03140527 about?

NCT03140527 is a clinical study titled "Study Assessing the Safety, Tolerability, Pharmacokinetics, Food Effect, and Drug-Drug Interactions of PTI-801 in Healthy Volunteers, and Safety, Tolerability, and Pharmacokinetics of PTI-801 in Subjects With Cystic Fibrosis". This trial will consist of two parts: Part 1 and Part 2. Part 1 will enroll adult healthy volunteers (HV) into four treatment groups. The first group will enroll HV into a single ascending dose (SAD) treatment group consisting of three cohorts. The second group will enroll HV into a multiple ascendi...

What is the current status of trial NCT03140527?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 171 participants. The study started on 2017-04-10. Estimated completion is 2020-02-27.

What conditions does trial NCT03140527 study?

This clinical trial studies the following conditions: Cystic Fibrosis, Healthy Volunteer.

What interventions are being tested in trial NCT03140527?

The interventions under investigation include: Placebo (DRUG), PTI-808 (DRUG), PTI-801 (DRUG).

Who is sponsoring clinical trial NCT03140527?

This trial is sponsored by Proteostasis Therapeutics, which has 5 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03140527 being conducted?

This trial has 20 study locations across Alabama, Alaska, California, Colorado, Florida. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Cystic Fibrosis

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT03140527's enrollment target sits among peer trials

171 39th of 169 higher than 131 of 169 other Cystic Fibrosis trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Cystic Fibrosis trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT03140527, the US trial registry maintained by the National Library of Medicine. NCT03140527 (mid enrollment · wide site footprint · completed) retrieved and formatted by PlainTrial, see methodology.