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NCT02829268 · ClinicalTrials.gov registry record · Phase 1

A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome

A Phase 1 study of Diabetes Mellitus and Ataxia, sponsored by Washington University School of Medicine.

Completed
Registry status
Phase 1
Development phase
21
Enrollment target
1
Study location

NCT02829268 is a Phase 1 study of Diabetes Mellitus and Ataxia that has completed, run by Washington University School of Medicine. The registered enrollment target is 21 participants, below the 1,867-participant average among 208 other Diabetes Mellitus trials with a reported enrollment target (99% lower). The trial reports 1 study location across 1 state.

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The verdict

NCT02829268, a Phase 1 study of Diabetes Mellitus and Ataxia, has completed, sponsored by Washington University School of Medicine.

COMPLETED
Registry status
Phase 1
Development phase
21 participants
Enrollment target
1
Study location

Study Summary

Wolfram syndrome is a rare genetic disorder characterized by juvenile-onset diabetes mellitus, diabetes insipidus, optic nerve atrophy, hearing loss, and neurodegeneration. The purpose of this study is to assess the safety and tolerability of dantrolene sodium in patients with Wolfram syndrome. In addition, we will assess the efficacy of dantrolene sodium on the cardinal manifestations of Wolfram syndrome, including visual acuity, remaining beta cell functions, and neurological functions. There is a screening period up to 56 days, a 6-month treatment period with an optional extension phase up to 24 months, and a 4-week safety follow-up period. Study assessments include medical \& medication history, physical exams, neurological exams, eye exams, endocrine exams, vital signs, height, weight, electrocardiograms, blood and urine tests, pregnancy test if applicable, and questionnaires.

Interventions

  • DRUG dantrolene sodium

Study Locations (1)

Missouri

  • Washington University School of Medicine - St Louis

Trial Details

FieldValue
Enrollment Target 21 participants
Start Date 2017-01
Est. Completion 2023-02
Phase Phase 1

What the Registry Record Tells You About NCT02829268

The ClinicalTrials.gov registry entry for NCT02829268 describes a study currently listed as completed, categorized as Phase 1. The registered enrollment target is 21 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 1,867-participant average among 208 other Diabetes Mellitus trials with a reported enrollment target (99% lower). The listed sponsor is Washington University School of Medicine, which has 1,502 total studies on file at ClinicalTrials.gov.

The record links to 4 conditions, with Diabetes Mellitus appearing as the primary indexed condition, and to 1 intervention - of which dantrolene sodium is the first listed.

NCT02829268 reports 1 study location spanning 1 distinct geographic area - top geographies include Missouri.

Frequently Asked Questions

What is clinical trial NCT02829268 about?

NCT02829268 is a clinical study titled "A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome". Wolfram syndrome is a rare genetic disorder characterized by juvenile-onset diabetes mellitus, diabetes insipidus, optic nerve atrophy, hearing loss, and neurodegeneration. The purpose of this study is to assess the safety and tolerability of dantrolene sodium in patients with Wolfram syndrome. In a...

What is the current status of trial NCT02829268?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 21 participants. The study started on 2017-01. Estimated completion is 2023-02.

What conditions does trial NCT02829268 study?

This clinical trial studies the following conditions: Diabetes Mellitus, Ataxia, Wolfram Syndrome, Optic Nerve Atrophy.

What interventions are being tested in trial NCT02829268?

The interventions under investigation include: dantrolene sodium (DRUG).

Who is sponsoring clinical trial NCT02829268?

This trial is sponsored by Washington University School of Medicine, which has 1,502 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT02829268 being conducted?

This trial has 1 study location across Missouri. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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