Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT01568658 · ClinicalTrials.gov registry record

Genetic and Physical Study of Childhood Nerve and Muscle Disorders

A clinical trial of Muscular Dystrophies and Inherited Neuromuscular Conditions, sponsored by National Institute of Neurological Disorders and Stroke (NINDS).

Recruiting
Registry status
9,300
Enrollment target
1
Study location

NCT01568658 is a study of Muscular Dystrophies and Inherited Neuromuscular Conditions that is actively recruiting participants, run by National Institute of Neurological Disorders and Stroke (NINDS). The registered enrollment target is 9,300 participants, above the 53-participant average among 11 other Muscular Dystrophies trials with a reported enrollment target (17447% higher). The trial reports 1 study location across 1 state.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT01568658, a study of Muscular Dystrophies and Inherited Neuromuscular Conditions, is actively recruiting participants, sponsored by National Institute of Neurological Disorders and Stroke (NINDS).

RECRUITING
Registry status
9,300 participants
Enrollment target
1
Study location

Study Summary

Background: \- Some nerve and muscle disorders that start early in life (before age 25), like some forms of muscular dystrophy, can run in families. However, the genetic causes of these disorders are not known. Also, doctors do not fully understand how symptoms of these disorders change over time. Researchers want to learn more about genetic nerve and muscle disorders that start in childhood by studying affected people and their family members, as well as healthy volunteers. Objectives: \- To better understand nerve and muscle disorders that start early in life and run in families. Eligibility: * Individuals at least 4 weeks old with childhood-onset muscular and nerve disorders, including those who have a later onset of a disorder that typically has childhood onset. * Affected and unaffected family members of the individuals with muscular and nerve disorders. * Healthy volunteers at least 4 weeks old with no nerve or muscle disorders. Design: * Participants will be screened with a physical exam and medical history. Genetic information will be collected from blood, saliva, cheek swab, or skin samples. Urine samples may also be collected. * Healthy volunteers and unaffected family members will have imaging studies of the muscles. These studies will include magnetic resonance imaging (MRI) and ultrasound scans. Results will be compared with those from the affected participants. * All participants with nerve and muscle disorders will have multiple tests, including the following: * Imaging studies of the muscles, including ultrasound and MRI scans. * Imaging studies of the bones, such as x-rays and DEXA scans. * Heart and lung function tests. * Eye exams. * Nerve and muscle electrical activity tests and biopsies. * Video and photo image collection of affected muscles. * Speech, language, and swallowing evaluation. * Lumbar puncture to collect spinal fluid for study. * Tests of movement, attention, thinking, and coordination. * Participants with nerve and muscle di

Study Locations (1)

Maryland

  • National Institutes of Health Clinical Center - Bethesda

Trial Details

FieldValue
Enrollment Target 9,300 participants
Start Date 2012-03-20

What the Registry Record Tells You About NCT01568658

The ClinicalTrials.gov registry entry for NCT01568658 describes a study currently listed as recruiting, categorized as an unspecified phase. The registered enrollment target is 9,300 participants, a figure that helps gauge the scale of data the investigators plan to collect, above the 53-participant average among 11 other Muscular Dystrophies trials with a reported enrollment target (17447% higher). The listed sponsor is National Institute of Neurological Disorders and Stroke (NINDS), which has 567 total studies on file at ClinicalTrials.gov.

The record links to 5 conditions, with Muscular Dystrophies appearing as the primary indexed condition, and to 0 interventions.

NCT01568658 reports 1 study location spanning 1 distinct geographic area - top geographies include Maryland.

Frequently Asked Questions

What is clinical trial NCT01568658 about?

NCT01568658 is a clinical study titled "Genetic and Physical Study of Childhood Nerve and Muscle Disorders". Background: \- Some nerve and muscle disorders that start early in life (before age 25), like some forms of muscular dystrophy, can run in families. However, the genetic causes of these disorders are not known. Also, doctors do not fully understand how symptoms of these disorders change over time. ...

What is the current status of trial NCT01568658?

This trial is currently recruiting. The enrollment target is 9,300 participants. The study started on 2012-03-20.

What conditions does trial NCT01568658 study?

This clinical trial studies the following conditions: Muscular Dystrophies, Inherited Neuromuscular Conditions, Inherited Neuropathies, Muscle Myopathies, Hereditary Spastic Paraplegias.

Who is sponsoring clinical trial NCT01568658?

This trial is sponsored by National Institute of Neurological Disorders and Stroke (NINDS), which has 567 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT01568658 being conducted?

This trial has 1 study location across Maryland. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Muscular Dystrophies

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.