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NCT01047306 · ClinicalTrials.gov registry record
A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)
A clinical trial of Sanfilippo Syndrome Type A, sponsored by Shire.
- Completed
- Registry status
- 25
- Enrollment target
- 1
- Study location
NCT01047306 is a study of Sanfilippo Syndrome Type A that has completed, run by Shire. The registered enrollment target is 25 participants. The trial reports 1 study location across 1 state.
The verdict
NCT01047306, a study of Sanfilippo Syndrome Type A, has completed, sponsored by Shire.
- COMPLETED
- Registry status
- 25 participants
- Enrollment target
- 1
- Study location
Study Summary
The purpose is to evaluate the course of disease progression in MPS IIIA patients who are untreated to identify potential surrogate endpoints that may be utilized in future ERT trials of MPS IIIA via defined assessments including standardized clinical, biochemical, neurocognitive, behavioral, developmental, and imaging measures.
Conditions Studied
Interventions
- OTHER assessment
Study Locations (1)
Minnesota
- University of Minnesota - Minneapolis
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 25 participants |
| Start Date | 2010-02-15 |
| Est. Completion | 2013-07-10 |
Interested in This Trial?
Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT01047306
The ClinicalTrials.gov registry entry for NCT01047306 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 25 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Shire, which has 245 total studies on file at ClinicalTrials.gov.
The record links to 1 condition, with Sanfilippo Syndrome Type A appearing as the primary indexed condition, and to 1 intervention - of which assessment is the first listed.
NCT01047306 reports 1 study location spanning 1 distinct geographic area - top geographies include Minnesota.
Frequently Asked Questions
What is clinical trial NCT01047306 about?
NCT01047306 is a clinical study titled "A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)". The purpose is to evaluate the course of disease progression in MPS IIIA patients who are untreated to identify potential surrogate endpoints that may be utilized in future ERT trials of MPS IIIA via defined assessments including standardized clinical, biochemical, neurocognitive, behavioral, develo...
What is the current status of trial NCT01047306?
This trial is currently completed. The enrollment target is 25 participants. The study started on 2010-02-15. Estimated completion is 2013-07-10.
What conditions does trial NCT01047306 study?
This clinical trial studies the following conditions: Sanfilippo Syndrome Type A.
What interventions are being tested in trial NCT01047306?
The interventions under investigation include: assessment (OTHER).
Who is sponsoring clinical trial NCT01047306?
This trial is sponsored by Shire, which has 245 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT01047306 being conducted?
This trial has 1 study location across Minnesota. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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