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NCT00443066 · ClinicalTrials.gov registry record
Clinical Study of Spinal Muscular Atrophy
A clinical trial of Spinal Muscular Atrophy, sponsored by Columbia University.
- Completed
- Registry status
- 120
- Enrollment target
- 1
- Study location
NCT00443066: Completed study of Spinal Muscular Atrophy, sponsored by Columbia University.
NCT00443066 is a study of Spinal Muscular Atrophy that has completed, run by Columbia University. The registered enrollment target is 120 participants, above the 104-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (15% higher). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT00443066, a study of Spinal Muscular Atrophy, has completed, sponsored by Columbia University.
- COMPLETED
- Registry status
- 120 participants
- Enrollment target
- 1
- Study location
Study Summary
The investigators propose to prepare for clinical trials where SMA patients are asked to join the research effort. The visits will include questions, physical exam, blood drawing, and sometimes X-rays and a skin biopsy. The investigators will use modern computer methods to process the information during which the investigators will plan a clinical trial. Once the clinical trial begins, the investigators will offer SMA patients participation if they meet the criteria for that trial. Identifying an effective SMA treatment is very important because there is currently none. Clinical trials are the only way to decide whether a new treatment works in SMA patients or not.
Primary Outcome
For SMAII/III patients over 2 years of age, we will additionally administer the Hammersmith SMA functional motor scale (H-SMA-FMS), a disease-specific instrument.
Conditions Studied
Study Locations (1)
New York
- Columbia University SMA Clinical Research Center - New York
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 120 participants |
| Start Date | 2005-05 |
| Est. Completion | 2011-08-17 |
What the finished NCT00443066 record still lists
NCT00443066 is an observational study that tracks outcomes without assigning an intervention. The registered 120 participants enrollment target is mid-sized for trials with a published cap, above the 104-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (15% higher).
The record links to 1 condition, with Spinal Muscular Atrophy appearing as the primary indexed condition, and to 0 interventions.
NCT00443066 reports a single indexed study location in New York.
Frequently Asked Questions
What is clinical trial NCT00443066 about?
NCT00443066 is a clinical study titled "Clinical Study of Spinal Muscular Atrophy". The investigators propose to prepare for clinical trials where SMA patients are asked to join the research effort. The visits will include questions, physical exam, blood drawing, and sometimes X-rays and a skin biopsy. The investigators will use modern computer methods to process the information du...
What is the current status of trial NCT00443066?
This trial is currently completed. The enrollment target is 120 participants. The study started on 2005-05. Estimated completion is 2011-08-17.
What conditions does trial NCT00443066 study?
This clinical trial studies the following conditions: Spinal Muscular Atrophy.
Who is sponsoring clinical trial NCT00443066?
This trial is sponsored by Columbia University, which has 958 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT00443066 being conducted?
This trial has 1 study location across New York. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
Learn More About Clinical Trials
Similar trials for Spinal Muscular Atrophy
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Where NCT00443066's enrollment target sits among peer trials
120 9th of 22 higher than 14 of 22 other Spinal Muscular Atrophy trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Spinal Muscular Atrophy trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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