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NCT00001671 · ClinicalTrials.gov registry record
The Classification and Cause of Leukodystrophies of Unknown Cause
A clinical trial of Lysosomal Storage Disease, sponsored by National Institute of Neurological Disorders and Stroke (NINDS).
- Completed
- Registry status
- 400
- Enrollment target
- 5
- Study locations
NCT00001671: Completed study of Lysosomal Storage Disease, sponsored by National Institute of Neurological Disorders and Stroke (NINDS).
NCT00001671 is a study of Lysosomal Storage Disease that has completed, run by National Institute of Neurological Disorders and Stroke (NINDS). The registered enrollment target is 400 participants. The trial reports 5 study locations across 4 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT00001671, a study of Lysosomal Storage Disease, has completed, sponsored by National Institute of Neurological Disorders and Stroke (NINDS).
- COMPLETED
- Registry status
- 400 participants
- Enrollment target
- 5
- Study locations
Study Summary
Leukodystrophy is a disease of the white matter of the brain. White matter is the portion of the brain responsible for conducting electrical impulses from one area of the brain to the other. Insulating cells called myelin cover the brain and nerve cells in the white matter. If myelin becomes damaged electrical information cannot be transferred properly. Many patients suffering from leukodystrophies do not fit the description of any of the defined types of leukodystrophies and are therefore considered to have a leukodystrophy of unknown cause. The purpose of this study is to define groups of patients with leukodystrophies and to work toward finding the cause of the disorders. In order to do this, researchers will analyze patients with leukodystrophies of unknown causes. Patients will undergo clinical, neurophysiologic, biochemical, and genetic examinations and tests. Researchers believe that by studying these patients and their disorders they will be able to better understand the causes of myelin destruction, and eventually lead to effective treatments for these disorders.
Conditions Studied
Study Locations (5)
Other
- Tel Aviv University - Tel Aviv
- Academiseh Ziuekenhuis Vrije Universiteit - Amsterdam
California
- University of California, San Francisco - San Francisco
District of Columbia
- Childrens National Medical Center - Washington D.C.
Cedex
- Institut National de la Sante' et de la Recherche Medicale - Clermont-Ferrand
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 400 participants |
| Start Date | 1997-09-09 |
| Est. Completion | 2008-12-15 |
What the finished NCT00001671 record still lists
NCT00001671 is an observational study that tracks outcomes without assigning an intervention. The registered 400 participants enrollment target is mid-sized for trials with a published cap.
The record links to 1 condition, with Lysosomal Storage Disease appearing as the primary indexed condition, and to 0 interventions.
NCT00001671 lists 5 locations in 4 states (Other, California, District of Columbia).
Frequently Asked Questions
What is clinical trial NCT00001671 about?
NCT00001671 is a clinical study titled "The Classification and Cause of Leukodystrophies of Unknown Cause". Leukodystrophy is a disease of the white matter of the brain. White matter is the portion of the brain responsible for conducting electrical impulses from one area of the brain to the other. Insulating cells called myelin cover the brain and nerve cells in the white matter. If myelin becomes damaged...
What is the current status of trial NCT00001671?
This trial is currently completed. The enrollment target is 400 participants. The study started on 1997-09-09. Estimated completion is 2008-12-15.
What conditions does trial NCT00001671 study?
This clinical trial studies the following conditions: Lysosomal Storage Disease.
Who is sponsoring clinical trial NCT00001671?
This trial is sponsored by National Institute of Neurological Disorders and Stroke (NINDS), which has 567 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT00001671 being conducted?
This trial has 5 study locations across California, District of Columbia, Cedex. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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