Ultragenyx Pharmaceutical
Ultragenyx Pharmaceutical sponsors 52 registered US clinical trials on ClinicalTrials.gov, 4 of them currently recruiting, and 25 completed. 9 of these trials are in Phase 3-4 (later-stage) and 24 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Long-chain Fatty Acid Oxidation Disorders (LC-FAOD), with 3 trials.
Trial Pipeline
52 total, page 2 of 2
Safety and Efficacy of Multiple Dosing Regimens of BPS804 in Post Menopausal Women With Low Bone Mineral Density
NCT01406548
Safety, Pharmacokinetics and Pharmacodynamics of BPS804 in Osteogenesis Imperfecta
NCT01417091
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 1 | 9 |
| Phase 2 | 15 |
| Phase 3 | 9 |
Therapeutic Areas
What the Pipeline for Ultragenyx Pharmaceutical Shows
According to the ClinicalTrials.gov registry, Ultragenyx Pharmaceutical is linked to 52 US clinical trials across every stage of research activity. Of those, 4 studies are currently recruiting, about 8% of the sponsor's indexed portfolio, and 25 are already marked complete, representing roughly 48% of the total.
The phase mix for Ultragenyx Pharmaceutical reports 9 late-stage studies (Phase 3 and Phase 4 combined) and 24 earlier-phase studies (Phase 1 and Phase 2).
The top therapeutic focus area indexed for Ultragenyx Pharmaceutical is Long-chain Fatty Acid Oxidation Disorders (LC-FAOD) with 3 linked trials, and 9 other condition areas appear in the top list above.
How to read these pipeline numbers
Recruiting share is one of the more practical signals here: it reflects how much of a sponsor's research is presently open to new participants, while the completed share indicates the depth of finished work that has already contributed registry results. Both counts come directly from the public ClinicalTrials.gov dataset and are refreshed on the registry side; this page mirrors the latest data pull without altering it.
A portfolio weighted toward Phase 3 usually reflects an organization advancing candidates toward regulatory review, where the research centers on comparative efficacy and broader safety across larger populations. A heavier Phase 1 and Phase 2 tilt generally indicates exploratory work, safety, dosing, and early signal detection, and is common among research-forward sponsors that seed many early programs. Phase 4 entries, when present, track interventions already in real-world use and typically focus on long-term safety, effectiveness across subgroups, or formulation comparisons.
That distribution is a quick read of where the organization concentrates its research attention; it does not imply product availability, market share, or any clinical endorsement. All numbers on this page come from ClinicalTrials.gov maintained by the National Library of Medicine, and counts can shift as new studies are registered or existing ones update their status. This information is provided for reference and educational purposes only, not as medical, investment, or regulatory advice, verify current details directly with ClinicalTrials.gov before relying on any figure here.
Read our methodology - how this data is sourced, computed, and verified.
Related
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page aggregates every registered trial from this sponsor, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.