Mirum Pharmaceuticals

Open enrollment with an early-phase pipeline tilt

According to ClinicalTrials.gov-derived indexes, Mirum Pharmaceuticals sits in the top decile of US sponsors by registered trial count (#568 of 15,742 sponsors by registered trial count).

28 total trials 5 currently recruiting 18 completed early-phase tilt top decile by trial count

Mirum Pharmaceuticals: 28 sponsored US clinical trials, 5 recruiting.

Mirum Pharmaceuticals sponsors 28 registered US clinical trials on ClinicalTrials.gov, 5 of them currently recruiting, and 18 completed. 8 of these trials are in Phase 3-4 (later-stage) and 17 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Progressive Familial Intrahepatic Cholestasis (PFIC), with 2 trials.

Top-decile sponsor footprint

Mirum Pharmaceuticals ranks in the top decile of sponsors by registered trial count (#568 of 15,742 sponsors by registered trial count). Volume at this scale usually reflects a long institutional pipeline, read phase tilt and therapeutic areas below before treating it as current-year activity.

Trial completion reliability score

C 65/100

18 of 20 decided trials (Completed vs. Terminated on ClinicalTrials.gov) reached their planned completion (90.0%), vs. national p10 68.4% / p90 100% among 1,234 sponsors with at least 10 decided trials. Still-open trials (Recruiting, Active-not-recruiting, Not-yet-recruiting) are excluded since they have not reached an outcome yet.

Open and recent trials

28 total, page 1 of 1

RECRUITING Phase 3

A Trial Evaluating Brelovitug vs Delayed Treatment for the Treatment of Chronic Hepatitis Delta Infection (AZURE-4)

NCT07298330

RECRUITING Phase 2

Study of MRM-3379 in Male Participants With Fragile X Syndrome (BLOOM)

NCT07209462

RECRUITING Phase 3

Evaluation of Maralixibat in Pruritus Associated With General Cholestatic Liver Disease (EXPAND)

NCT06553768

RECRUITING

Long-Term SafEty and Clinical Outcomes of LivmArli in Patients in the United States (LEAP-US)

NCT06193928

RECRUITING Phase 2

A Study to Evaluate Efficacy and Safety of an Investigational Drug Named Volixibat in Patients With Itching Caused by Primary Biliary Cholangitis

NCT05050136

ACTIVE NOT RECRUITING Phase 2

A Trial Evaluating BJT-778 vs Delayed Treatment for the Treatment of Chronic Hepatitis Delta Infection

NCT06907290

ACTIVE NOT RECRUITING Phase 2

A Study to Evaluate Efficacy and Safety of an Investigational Drug Named Volixibat in Patients With Itching Caused by Primary Sclerosing Cholangitis (PSC)

NCT04663308

ACTIVE NOT RECRUITING

The REPLACE Registry for Cholbam® (Cholic Acid)

NCT03115086

COMPLETED Phase 2

A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).

NCT04729751

COMPLETED Phase 2

Evaluation of Maralixibat in Biliary Atresia Response Post-Kasai

NCT04524390

TERMINATED Phase 2

A Placebo-controlled Study of Volixibat in Subjects With Elevated Serum Bile Acids Associated With Intrahepatic Cholestasis of Pregnancy (OHANA)

NCT04718961

COMPLETED Phase 3

Study to Evaluate Patients With Cerebrotendinous Xanthomatosis (RESTORE)

NCT04270682

COMPLETED Phase 2

MRX-800: A Long-Term Safety Study of Maralixibat in the Treatment of Cholestatic Liver Disease in Subjects Who Previously Participated in a Maralixibat Study

NCT04168385

COMPLETED Phase 3

An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC)

NCT04185363

COMPLETED Phase 3

A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)

NCT03905330

TERMINATED Phase 2

Volixibat (SHP626) in the Treatment of Adults With Nonalcoholic Steatohepatitis (NASH)

NCT02787304

COMPLETED Phase 1

A Study to Investigate How the Study Drug SHP626 is Eliminated From the Body After One Dose

NCT02571192

COMPLETED Phase 1

Study to Assess the Relative Potency of Multiple Oral Doses of LUM001 and SHP626 in Overweight and Obese Adults as Assessed by Fecal Bile Acid Excretion

NCT02475317

COMPLETED Phase 2

An Extension Study to Evaluate the Long-Term Safety and Durability of Effect of LUM001 in the Treatment of Cholestatic Liver Disease in Pediatric Subjects With Alagille Syndrome

NCT02117713

COMPLETED Phase 1

Safety and Tolerability Study of SHP626 in Overweight and Obese Adults

NCT02287779

COMPLETED Phase 2

Evaluation of LUM001 in the Reduction of Pruritus in Alagille Syndrome

NCT02057692

COMPLETED

Validation of the Itch Reported Outcome (ItchRO) Diaries in Pediatric Cholestatic Liver Disease

NCT02131623

COMPLETED Phase 2

Open Label Study to Evaluate Efficacy and Long Term Safety of LUM001 (Maralixibat) in the Treatment of Cholestatic Liver Disease in Patients With Progressive Familial Intrahepatic Cholestasis

NCT02057718

COMPLETED Phase 2

Open Label Study to Evaluate Safety and Efficacy of LUM001 in Patients With Primary Sclerosing Cholangitis

NCT02061540

COMPLETED Phase 2

Phase 2 Study to Evaluate LUM001 in Combination With Ursodeoxycholic Acid in Patients With Primary Biliary Cirrhosis

NCT01904058

COMPLETED Phase 3

Efficacy of To Be Marketed (TBM) Cholic Acid Capsules Used to Treat Children With Inborn Errors of Bile Acid Synthesis

NCT01115582

COMPLETED Phase 3

Open Label, Continuation Study of Cholic Acid in Subjects With Inborn Errors of Bile Acid Synthesis

NCT01438411

COMPLETED Phase 3

Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

NCT00007020

What is open in the Mirum Pharmaceuticals pipeline

5 recruiting of 28 indexed (18% open); 18 completed (64%).

Phase mix: 8 late (III/IV) vs 17 early (I/II) (early-phase heavy).

Top condition: Progressive Familial Intrahepatic Cholestasis (PFIC) (2 trials), 9 others listed.

How open-pipeline share is computed

Recruiting share is recruiting_count divided by trial_count for this sponsor in the public registry export. Status can change between pulls; treat the figure as a research-attention snapshot, not product availability.

Mirum Pharmaceuticals: open-pipeline peers nationwide

Peers matched on 28 registered trials and 18% open enrollment, not the therapeutic-area sidebar.

Mirum Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot). 2×2 strategic matrix plotting 9 entities by Total trials (X) and Recruiting share (Y), with a crosshair dividing the plot into four quadrants. Higher volume & more openFocused & more openHigher volume, mostly closedSmaller & mostly closed 05001,0001,500 0%5%10%15%20%25% Total trials Recruiting share Mirum PharmaceuticalsAxsome TherapeuticsBenaroya Research InstituteCAMC Health SystemCTI BioPharmaKite, A Gilead CompanyColumbia UniversityWest Virginia UniversityHospital for Special Surgery, New York
Mirum Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot).

Mirum Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together.

Sponsors near 28 trials (± recruiting share)

Sponsors near 18% open enrollment (± trial volume)

What to do with this Mirum Pharmaceuticals page

28 registered trials is a research-attention snapshot, not an endorsement of Mirum Pharmaceuticals or any single study.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Mirum Pharmaceuticals pipeline card: 28 registered trials from official public datasets.Report a data error.