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NCT04185363 · ClinicalTrials.gov registry record · Phase 3

An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC)

A Phase 3 study of Progressive Familial Intrahepatic Cholestasis (PFIC), sponsored by Mirum Pharmaceuticals.

Completed
Registry status
Phase 3
Development phase
90
Enrollment target
20
Study locations

NCT04185363 is a Phase 3 study of Progressive Familial Intrahepatic Cholestasis (PFIC) that has completed, run by Mirum Pharmaceuticals. The registered enrollment target is 90 participants. The trial reports 20 study locations across 11 states.

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The verdict

NCT04185363, a Phase 3 study of Progressive Familial Intrahepatic Cholestasis (PFIC), has completed, sponsored by Mirum Pharmaceuticals.

COMPLETED
Registry status
Phase 3
Development phase
90 participants
Enrollment target
20
Study locations

Study Summary

The primary objective of this open label extension study is to evaluate the long-term safety and tolerability of maralixibat.

Interventions

  • DRUG Maralixibat

Study Locations (20)

Other

  • Hospital Italiano de Buenos Aires - Buenos Aires
  • Medizinische Universität Wien, Universitätsklinik für Kinder- und Jugendheilkunde - Vienna
  • Cliniques Universitaires Saint-Luc - Brussels
  • Sociedade Beneficente de Senhoras Hospital Sírio-Libanês - São Paulo
  • Fundacion Cardioinfantil - Bogotá
  • Groupement Hospitalier Est Hopital, Femme Mère Enfant de Lyon - Lyon
  • CHU de Toulouse - Hôpital des Enfants - Toulouse
  • Medizinische Hochschule - Hanover
  • Azienda Ospedaliera Papa Giovanni XXIII - Unita di Pediatria - Bergamo

Texas

  • University of Texas Southwestern Medical Center - Dallas
  • University of Texas, Health Science Center San Antonio - San Antonio

California

  • Children's Hospital Los Angeles - Los Angeles

District of Columbia

  • Medstar Georgetown University Hospital - Washington D.C.

Florida

  • Advent Health - Orlando

New York

  • Children's Hospital at Montefiore - The Bronx

Ohio

  • Cincinnati Children's Hospital - Cincinnati

Pennsylvania

  • Children Hospital of Pittsburgh - Pittsburgh

Trial Details

FieldValue
Enrollment Target 90 participants
Start Date 2020-01-08
Est. Completion 2025-04-23
Phase Phase 3

Sponsor

Mirum Pharmaceuticals

28 total trials

What the Registry Record Tells You About NCT04185363

The ClinicalTrials.gov registry entry for NCT04185363 describes a study currently listed as completed, categorized as Phase 3. The registered enrollment target is 90 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Mirum Pharmaceuticals, which has 28 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Progressive Familial Intrahepatic Cholestasis (PFIC) appearing as the primary indexed condition, and to 1 intervention - of which Maralixibat is the first listed.

NCT04185363 reports 20 study locations spanning 11 distinct geographic areas - top geographies include Other, Texas, California.

Frequently Asked Questions

What is clinical trial NCT04185363 about?

NCT04185363 is a clinical study titled "An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC)". The primary objective of this open label extension study is to evaluate the long-term safety and tolerability of maralixibat.

What is the current status of trial NCT04185363?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 90 participants. The study started on 2020-01-08. Estimated completion is 2025-04-23.

What conditions does trial NCT04185363 study?

This clinical trial studies the following conditions: Progressive Familial Intrahepatic Cholestasis (PFIC).

What interventions are being tested in trial NCT04185363?

The interventions under investigation include: Maralixibat (DRUG).

Who is sponsoring clinical trial NCT04185363?

This trial is sponsored by Mirum Pharmaceuticals, which has 28 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04185363 being conducted?

This trial has 20 study locations across California, District of Columbia, Florida, New York, Ohio. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.