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ClinicalTrials.gov 1 recruiting now early-phase tilt small index

Sphingolipidoses: early-phase trial registry

1 of 2 indexed Sphingolipidoses trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #7,188 of 28,707 conditions by registered trial count.

2 US clinical trials · 1 currently recruiting · #7,188 of 28,707 conditions by registered trial count

Sphingolipidoses: 2 US clinical trials tracked, 1 recruiting.

Sphingolipidoses is the subject of 2 registered US clinical trials on ClinicalTrials.gov, 1 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 1 in Phase 1-2 (earlier-stage). The most active sponsor is Masonic Cancer Center, University of Minnesota, running 1 of these trials.

Enrollment posture brief

Registry condition sphingolipidoses

OPEN 1 | RECR 50% | LATE 0 | EARLY 1 | RANK #7188 | SPON 1

Nearest open-share peer: Abdominal Aortic Aneurysms (50% recruiting · 6 trials)

Ablation80%ACL Reconstruction80%Abuse, Drug60%Acceptability60%Sphingolipidoses (this)50%
Open-enrollment share among volume-matched conditions near Sphingolipidoses

Sphingolipidoses lists 1 open slots (50% of 2 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Sphingolipidoses on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Sphingolipidoses is recruiting above its size-band peers.

    1 of 2 indexed trials (50%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

Phase 21

Phase Distribution

PhaseTrial count
Phase 2 1

Named interventions

Most-linked intervention names on Sphingolipidoses records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

cALD SR-A (Standard-Risk, Regimen A) Drug
1 trials
Osteopetrosis Haploidentical Only Preparative Regimen Drug
1 trials
Osteopetrosis Only Preparative Regimen Drug
1 trials
IMD Preparative Regimen Drug
1 trials
Stem Cell Transplantation Biological
1 trials
no intervention Other
1 trials

US sites by state

Facility locations filed on Sphingolipidoses trials. A trial with sites in several states counts in each.

Minnesota 1 trials
California 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Sphingolipidoses page

2 registered trials, 1 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Sphingolipidoses condition card totals 2 registered trials; most-linked intervention cALD SR-A (Standard-Risk, Regimen A); top US site state Minnesota. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.