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ClinicalTrials.gov enrollment closed early-phase tilt small index

Amaurosis of Leber: early-phase trial registry

A small indexed set (1 trial) with no open enrollment listed right now.

Corpus placement: #11,370 of 28,707 conditions by registered trial count.

1 US clinical trials · none currently recruiting · #11,370 of 28,707 conditions by registered trial count

Amaurosis of Leber: 1 US clinical trial tracked, none currently recruiting.

Amaurosis of Leber is the subject of 1 registered US clinical trials on ClinicalTrials.gov, none currently recruiting. 0 are in Phase 3-4 (later-stage) and 1 in Phase 1-2 (earlier-stage). The most active sponsor is University of Pennsylvania, running 1 of these trials.

Enrollment posture brief

Registry condition amaurosis-of-leber

OPEN 0 | RECR 0% | LATE 0 | EARLY 1 | RANK #11370 | SPON 1

Nearest open-share peer: Accelerated Phase Chronic Myelogenous Leukemia (0% recruiting · 12 trials)

Ablation80%ACL Reconstruction80%Abuse, Drug60%Acceptability60%Amaurosis of Leber (this)0%
Open-enrollment share among volume-matched conditions near Amaurosis of Leber

Amaurosis of Leber has no open enrollment in this registry pull (1 archived studies). Peers show how other volume-matched labels compare on open share. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Amaurosis of Leber on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Amaurosis of Leber is recruiting below its size-band peers.

    0 of 1 indexed trials (0%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

Phase 11

Phase Distribution

PhaseTrial count
Phase 1 1

Top Sponsors

Named interventions

Most-linked intervention names on Amaurosis of Leber records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

rAAV2-CBSB-hRPE65 Genetic
1 trials

US sites by state

Facility locations filed on Amaurosis of Leber trials. A trial with sites in several states counts in each.

Pennsylvania 1 trials
Florida 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Amaurosis of Leber page

1 registered trials, 0 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • No Amaurosis of Leber trials are currently recruiting in this registry; that can change as new trials post, or check the broader research index. Browse research indexes
  • University of Pennsylvania sponsors the most Amaurosis of Leber trials on record, review their full trial history before evaluating a specific study. See University of Pennsylvania's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Amaurosis of Leber condition card totals 1 registered trials; most-linked intervention rAAV2-CBSB-hRPE65; top US site state Pennsylvania. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.