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NCT07218575 · ClinicalTrials.gov registry record · Phase 2

Double-Blind Trial of Everolimus for Improving Social Abilities in PTEN Germline Mutations

A Phase 2 study, sponsored by Boston Children's Hospital.

Not yet
Registry status
Phase 2
Development phase
60
Enrollment target

NCT07218575 is a Phase 2 study that has not yet begun recruiting, run by Boston Children's Hospital. The registered enrollment target is 60 participants.

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The verdict

NCT07218575, a Phase 2 study, has not yet begun recruiting, sponsored by Boston Children's Hospital.

NOT YET RECRUITING
Registry status
Phase 2
Development phase
60 participants
Enrollment target

Study Summary

The goal of this study is to examine the safety and treatment effects of everolimus in adults and children with PTEN Hamartoma Tumor Syndrome (PHTS) who experience social difficulties. The study will measure if everolimus can safely improve social abilities and functioning in this study population. PTEN Hamartoma Tumor Syndrome (PHTS) is a genetic condition that results from alteration (germline variant) to the PTEN gene. It is associated with a wide range of symptoms and characteristics, which vary from individual to individual. These include symptoms such as harmatomas (non-cancerous lesions), an increased risk of certain types of cancer, having a larger than average head, and abnormalities in blood vessels. Some people also have neurobehavioral problems including social difficulties. It is estimated approximately 25% (1 in 4) of people with PHTS meet the criteria for an autism diagnosis. The study lasts for one year. In the first 6 months half of participants will receive everolimus as a once daily oral tablet, and half will receive placebo tablets. For the second 6 months all participants will receive everolimus. Visits to the study clinic are required at the start, month 3, month 6, month 9 and month 12, with phone calls or virtual visits in between. Assessments include questionnaires, blood tests and urine tests, physical and neurological exams, and vital signs. Everolimus is an existing FDA approved medication used to treat other conditions, including a genetic condition called tuberous sclerosis complex which has some similarities to PHTS, and several types of cancer.

Interventions

  • DRUG Placebo
  • DRUG Everolimus blinded oral capsules

Trial Details

FieldValue
Enrollment Target 60 participants
Start Date 2026-09-01
Est. Completion 2030-09
Phase Phase 2

Sponsor

Boston Children's Hospital

462 total trials

What the Registry Record Tells You About NCT07218575

The ClinicalTrials.gov registry entry for NCT07218575 describes a study currently listed as not yet recruiting, categorized as Phase 2. The registered enrollment target is 60 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Boston Children's Hospital, which has 462 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 2 interventions - of which Placebo is the first listed.

NCT07218575 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT07218575 about?

NCT07218575 is a clinical study titled "Double-Blind Trial of Everolimus for Improving Social Abilities in PTEN Germline Mutations". The goal of this study is to examine the safety and treatment effects of everolimus in adults and children with PTEN Hamartoma Tumor Syndrome (PHTS) who experience social difficulties. The study will measure if everolimus can safely improve social abilities and functioning in this study population. ...

What is the current status of trial NCT07218575?

This trial is currently not yet recruiting. It is a Phase 2 study. The enrollment target is 60 participants. The study started on 2026-09-01. Estimated completion is 2030-09.

What interventions are being tested in trial NCT07218575?

The interventions under investigation include: Placebo (DRUG), Everolimus blinded oral capsules (DRUG).

Who is sponsoring clinical trial NCT07218575?

This trial is sponsored by Boston Children's Hospital, which has 462 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.