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RECRUITING

Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy

NCT06503367 · View on ClinicalTrials.gov ↗

Study Summary

The goal of this observational study is to understand how young children with LAMA2-related dystrophy move and change over time. We will also learn about how this condition impacts other body systems. Participants will undergo: * Neuromuscular assessments * Blood collections * Swallowing and breathing assessments * Questionnaires

Study Locations (14)

California

  • University of California, Los Angeles — Los Angeles
  • Stanford University — Stanford

Ohio

  • Cincinnati Children's Hospital Medical Center — Cincinnati
  • Nationwide Children's Hospital — Columbus

Illinois

  • Ann & Robert H. Lurie Children's Hospital of Chicago — Chicago

Iowa

  • University of Iowa Stead Family Children's Hospital — Iowa City

Maryland

  • National Institute of Neurological Disorders and Stroke, NIH — Bethesda

Massachusetts

  • Boston Children's Hospital — Boston

Minnesota

  • University of Minnesota — Saint Paul

Missouri

  • Washington University in St. Louis — St Louis

Trial Details

FieldValue
Enrollment Target 44 participants
Start Date 2025-05-12
Est. Completion 2028-09

Sponsor

Nationwide Children's Hospital

239 total trials

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Full Details on ClinicalTrials.gov ↗

What the Registry Record Tells You About NCT06503367

The ClinicalTrials.gov registry entry for NCT06503367 describes a study currently listed as recruiting. It is categorized as an unspecified phase, which is the standard way researchers label where a study sits along the investigational pathway from early safety work through later efficacy and post-marketing evaluation. The registered enrollment target is 44 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Nationwide Children's Hospital, which has 239 total studies on file at ClinicalTrials.gov, and sponsors are the parties responsible for study design, oversight, and regulatory filings.

The record links to 1 condition, with LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\) appearing as the primary indexed condition, and to 0 interventions. Interventions can include drugs, devices, procedures, behavioral programs, or observational arms, and each is tracked as a separate registry field so that downstream queries can filter accurately. When a trial lists multiple interventions, it usually reflects a multi-arm design or a comparison protocol rather than a single treatment being tested in isolation. The brief summary published in the registry is the clearest source of protocol intent and should be read before drawing conclusions from any sidebar tags.

Geographic footprint matters for practical reasons: NCT06503367 reports 14 study locations spanning 12 distinct geographic areas — top geographies include California, Ohio, Illinois. A larger site network tends to correlate with broader recruitment capacity, but it does not imply anything about study quality, and site-level enrollment status can diverge from the overall registry status shown above. Every data point on this page comes from the public ClinicalTrials.gov dataset and is reproduced here for reference only; it is not a medical recommendation, an endorsement of the sponsor, or an invitation to enroll. Verify current status, eligibility criteria, and contact details directly at ClinicalTrials.gov, and discuss any participation decision with your own healthcare provider.

Frequently Asked Questions

What is clinical trial NCT06503367 about?

NCT06503367 is a clinical study titled "Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy". The goal of this observational study is to understand how young children with LAMA2-related dystrophy move and change over time. We will also learn about how this condition impacts other body systems. Participants will undergo: * Neuromuscular assessments * Blood collections * Swallowing and breat...

What is the current status of trial NCT06503367?

This trial is currently recruiting. The enrollment target is 44 participants. The study started on 2025-05-12. Estimated completion is 2028-09.

What conditions does trial NCT06503367 study?

This clinical trial studies the following conditions: LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\). These conditions were identified from the trial registry and reflect the primary focus areas of the research.

Who is sponsoring clinical trial NCT06503367?

This trial is sponsored by Nationwide Children's Hospital, which has 239 total clinical trials registered on ClinicalTrials.gov. The sponsor is responsible for the study's design, funding, and regulatory compliance.

Where is trial NCT06503367 being conducted?

This trial has 14 study locations across California, Illinois, Iowa, Maryland, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Related

Data sourced from official U.S. government datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial