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NCT05298358 · ClinicalTrials.gov registry record · Phase 1

RIC alloBMT With Post-transplant Cyclophosphamide for Refractory Systemic Sclerosis

A Phase 1 study, sponsored by Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins.

Terminated
Registry status
Phase 1
Development phase
1
Enrollment target

NCT05298358 is a Phase 1 study that was terminated before completion, run by Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins. The registered enrollment target is 1 participants.

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The verdict

NCT05298358, a Phase 1 study, was terminated before completion, sponsored by Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins.

TERMINATED
Registry status
Phase 1
Development phase
1 participants
Enrollment target

Study Summary

This is a Phase I, single arm, open label, single center pilot study to assess a reduced-intensity conditioning regimen, bone marrow transplantation with high dose cyclophosphamide (PTCy) in recipients with refractory systemic sclerosis. This study expects to enroll 15 donor/recipient pairs for a total of 30 participants. The primary objective of this study is to assess the safety of using a reduced intensity condition (RIC) preparative regimen bone marrow transplant (BMT) with post-transplant cyclophosphamide for graft vs host disease (GVHD) prophylaxis as treatment for patients with scleroderma. Safety events are grade III-IV GVHD and treatment related mortality within 1 year. Eligibility includes patients \>18 years who are eligible for transplantation according to the BMT Policy Manual, meet the 2013 ACR/EULAR Criteria for Systemic Sclerosis and display active diffuse cutaneous disease. The trial also includes analyses of the effects of BMT on skeletal and cardiac muscle using systemic scleroderma serum biomarkers of CK, aldolase, and troponin as well as periodic monitoring of circulating scleroderma auto-antibody titers, autoreactive T cells, and flow cytometric signatures over the one-year study period to correlate with response.

Interventions

  • BIOLOGICAL RIC alloBMT w PTCy in refractory SSc

Trial Details

FieldValue
Enrollment Target 1 participants
Start Date 2022-11-18
Est. Completion 2024-11-21
Phase Phase 1

What the Registry Record Tells You About NCT05298358

The ClinicalTrials.gov registry entry for NCT05298358 describes a study currently listed as terminated, categorized as Phase 1. The registered enrollment target is 1 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins, which has 523 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 1 intervention - of which RIC alloBMT w PTCy in refractory SSc is the first listed.

NCT05298358 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT05298358 about?

NCT05298358 is a clinical study titled "RIC alloBMT With Post-transplant Cyclophosphamide for Refractory Systemic Sclerosis". This is a Phase I, single arm, open label, single center pilot study to assess a reduced-intensity conditioning regimen, bone marrow transplantation with high dose cyclophosphamide (PTCy) in recipients with refractory systemic sclerosis. This study expects to enroll 15 donor/recipient pairs for a to...

What is the current status of trial NCT05298358?

This trial is currently terminated. It is a Phase 1 study. The enrollment target is 1 participants. The study started on 2022-11-18. Estimated completion is 2024-11-21.

What interventions are being tested in trial NCT05298358?

The interventions under investigation include: RIC alloBMT w PTCy in refractory SSc (BIOLOGICAL).

Who is sponsoring clinical trial NCT05298358?

This trial is sponsored by Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins, which has 523 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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