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NCT04823143 · ClinicalTrials.gov registry record
Natural History Study of Patients With VCP-related Disease
A clinical trial of IBMPFD, sponsored by Nationwide Children's Hospital.
- Active
- Registry status
- 44
- Enrollment target
- 1
- Study location
NCT04823143: Active study of IBMPFD, sponsored by Nationwide Children's Hospital.
NCT04823143 is a study of IBMPFD that is active but no longer recruiting, run by Nationwide Children's Hospital. The registered enrollment target is 44 participants. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04823143, a study of IBMPFD, is active but no longer recruiting, sponsored by Nationwide Children's Hospital.
- ACTIVE NOT RECRUITING
- Registry status
- 44 participants
- Enrollment target
- 1
- Study location
Study Summary
A natural history study to understand the expected progression of disease in patients with confirmed mutations in the VCP gene over 1 year.
Primary Outcome
Patients will complete 100-meter walk/run on a 25-meter course as quickly as possible, safely. The time to complete is recorded.
Conditions Studied
Study Locations (1)
Ohio
- Nationwide Children's Hospital - Columbus
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 44 participants |
| Start Date | 2021-03-18 |
| Est. Completion | 2025-09-01 |
What the registry record for NCT04823143 still lists
NCT04823143 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 44 participants, a relatively small participant target.
The record links to 1 condition, with IBMPFD appearing as the primary indexed condition, and to 0 interventions.
NCT04823143 reports a single indexed study location in Ohio.
Frequently Asked Questions
What is clinical trial NCT04823143 about?
NCT04823143 is a clinical study titled "Natural History Study of Patients With VCP-related Disease". A natural history study to understand the expected progression of disease in patients with confirmed mutations in the VCP gene over 1 year.
What is the current status of trial NCT04823143?
This trial is currently active not recruiting. The enrollment target is 44 participants. The study started on 2021-03-18. Estimated completion is 2025-09-01.
What conditions does trial NCT04823143 study?
This clinical trial studies the following conditions: IBMPFD.
Who is sponsoring clinical trial NCT04823143?
This trial is sponsored by Nationwide Children's Hospital, which has 188 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04823143 being conducted?
This trial has 1 study location across Ohio. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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