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NCT04641442 · ClinicalTrials.gov registry record · Phase 2

Study to Evaluate the Efficacy, Safety and Tolerability of MAS825 in Patients With Monogenic IL-18 Driven Autoinflammatory Diseases, Including NLRC4-GOF, XIAP Deficiency, or CDC42 Mutations

A Phase 2 study of NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations, sponsored by Novartis Pharmaceuticals.

Active
Registry status
Phase 2
Development phase
17
Enrollment target
20
Study locations

NCT04641442 is a Phase 2 study of NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations that is active but no longer recruiting, run by Novartis Pharmaceuticals. The registered enrollment target is 17 participants. The trial reports 20 study locations across 8 states.

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The verdict

NCT04641442, a Phase 2 study of NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations, is active but no longer recruiting, sponsored by Novartis Pharmaceuticals.

ACTIVE NOT RECRUITING
Registry status
Phase 2
Development phase
17 participants
Enrollment target
20
Study locations

Study Summary

This study is a Phase 2 trial designed to evaluate the clinical efficacy, safety, and tolerability of MAS825 in patients with NLRC4-GOF, XIAP deficiency, or CDC42 mutations.

Interventions

  • BIOLOGICAL Placebo
  • BIOLOGICAL MAS825

Study Locations (20)

Other

  • Novartis Investigative Site - Prague
  • Novartis Investigative Site - Prague
  • Ustav Imunologie 2 LF UK a FN Motol - Prague
  • Novartis Investigative Site - Paris
  • Novartis Investigative Site - Chiba
  • Novartis Investigative Site - Madrid
  • Novartis Investigative Site - London
  • Great Ormond Street Hospital - London

Ohio

  • Cincinnati Children's Hospital - Cincinnati
  • Cincinnati Childrens Hospital - Cincinnati

Pennsylvania

  • Childrens Hospital of Philadelphia - Philadelphia
  • Children´s Hospital of Philadelphia - Philadelphia

Texas

  • Texas Childrens Hospital - Houston
  • Texas Children´s Hospital - Houston

Washington

  • Seattle Childrens Hospital - Seattle
  • Seattle Children´s Hospital - Seattle

RM

  • Bambino Gesu Hospital - Roma
  • Novartis Investigative Site - Roma

CZ

  • Centrum detske revmatologie a autoinflamatornich onemocneni - Prague

Catalonia

  • Hospital Clinic Barcelona - Barcelona

Trial Details

FieldValue
Enrollment Target 17 participants
Start Date 2020-12-18
Est. Completion 2032-04-07
Phase Phase 2

Sponsor

Novartis Pharmaceuticals

1,375 total trials

What the Registry Record Tells You About NCT04641442

The ClinicalTrials.gov registry entry for NCT04641442 describes a study currently listed as active not recruiting, categorized as Phase 2. The registered enrollment target is 17 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Novartis Pharmaceuticals, which has 1,375 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations appearing as the primary indexed condition, and to 2 interventions - of which Placebo is the first listed.

NCT04641442 reports 20 study locations spanning 8 distinct geographic areas - top geographies include Other, Ohio, Pennsylvania.

Frequently Asked Questions

What is clinical trial NCT04641442 about?

NCT04641442 is a clinical study titled "Study to Evaluate the Efficacy, Safety and Tolerability of MAS825 in Patients With Monogenic IL-18 Driven Autoinflammatory Diseases, Including NLRC4-GOF, XIAP Deficiency, or CDC42 Mutations". This study is a Phase 2 trial designed to evaluate the clinical efficacy, safety, and tolerability of MAS825 in patients with NLRC4-GOF, XIAP deficiency, or CDC42 mutations.

What is the current status of trial NCT04641442?

This trial is currently active not recruiting. It is a Phase 2 study. The enrollment target is 17 participants. The study started on 2020-12-18. Estimated completion is 2032-04-07.

What conditions does trial NCT04641442 study?

This clinical trial studies the following conditions: NLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 Mutations.

What interventions are being tested in trial NCT04641442?

The interventions under investigation include: Placebo (BIOLOGICAL), MAS825 (BIOLOGICAL).

Who is sponsoring clinical trial NCT04641442?

This trial is sponsored by Novartis Pharmaceuticals, which has 1,375 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04641442 being conducted?

This trial has 20 study locations across Ohio, Pennsylvania, Texas, Washington, CZ. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.