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NCT04580368 · ClinicalTrials.gov registry record · NA

Testing Drug Efficacy in Cystic Fibrosis Through N-of-1 Trials

A NA study of Cystic Fibrosis, sponsored by Children's Hospital Medical Center, Cincinnati.

Recruiting
Registry status
NA
Development phase
50
Enrollment target
1
Study location

NCT04580368 is a NA study of Cystic Fibrosis that is actively recruiting participants, run by Children's Hospital Medical Center, Cincinnati. The registered enrollment target is 50 participants, below the 179-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target (72% lower). The trial reports 1 study location across 1 state.

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The verdict

NCT04580368, a NA study of Cystic Fibrosis, is actively recruiting participants, sponsored by Children's Hospital Medical Center, Cincinnati.

RECRUITING
Registry status
NA
Development phase
50 participants
Enrollment target
1
Study location

Study Summary

The purpose of this study is to validate and utilize a personalized medicine approach to identify potential treatments with current FDA approved CFTR modifiers for non-approved CF gene mutations. The study will perform ex vivo testing of CFTR function and current marketed CFTR modulating drugs on expanded nasal cells at Cincinnati Children's Human Nasal Epithelium (HNE) Core Laboratory. The results will be confirmed and translated into bedside care through an N of 1 trial to determine effectiveness of treatment.

Conditions Studied

Interventions

  • DRUG CFTR Modulators

Study Locations (1)

Ohio

  • CCHMC - Cincinnati

Trial Details

FieldValue
Enrollment Target 50 participants
Start Date 2021-05-01
Est. Completion 2030-01-31
Phase NA

What the Registry Record Tells You About NCT04580368

The ClinicalTrials.gov registry entry for NCT04580368 describes a study currently listed as recruiting, categorized as NA. The registered enrollment target is 50 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 179-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target (72% lower). The listed sponsor is Children's Hospital Medical Center, Cincinnati, which has 571 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Cystic Fibrosis appearing as the primary indexed condition, and to 1 intervention - of which CFTR Modulators is the first listed.

NCT04580368 reports 1 study location spanning 1 distinct geographic area - top geographies include Ohio.

Frequently Asked Questions

What is clinical trial NCT04580368 about?

NCT04580368 is a clinical study titled "Testing Drug Efficacy in Cystic Fibrosis Through N-of-1 Trials". The purpose of this study is to validate and utilize a personalized medicine approach to identify potential treatments with current FDA approved CFTR modifiers for non-approved CF gene mutations. The study will perform ex vivo testing of CFTR function and current marketed CFTR modulating drugs on ex...

What is the current status of trial NCT04580368?

This trial is currently recruiting. It is a NA study. The enrollment target is 50 participants. The study started on 2021-05-01. Estimated completion is 2030-01-31.

What conditions does trial NCT04580368 study?

This clinical trial studies the following conditions: Cystic Fibrosis.

What interventions are being tested in trial NCT04580368?

The interventions under investigation include: CFTR Modulators (DRUG).

Who is sponsoring clinical trial NCT04580368?

This trial is sponsored by Children's Hospital Medical Center, Cincinnati, which has 571 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04580368 being conducted?

This trial has 1 study location across Ohio. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.