Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT04308954 · ClinicalTrials.gov registry record · Phase 1

Neuroimaging GABA Physiology in Fragile X Syndrome

A Phase 1 study, sponsored by Stanford University.

Terminated
Registry status
Phase 1
Development phase
17
Enrollment target

NCT04308954: Clinical Trial Phase 1 study, sponsored by Stanford University.

NCT04308954 is a Phase 1 study that was terminated before completion, run by Stanford University. The registered enrollment target is 17 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (72% lower). According to ClinicalTrials.gov, the official US trial registry.

View on ClinicalTrials.gov ↗

View your shortlist → Add completion date to calendar (.ics) →

The verdict

NCT04308954, a Phase 1 study, was terminated before completion, sponsored by Stanford University.

TERMINATED
Registry status
Phase 1
Development phase
17 participants
Enrollment target

Study Summary

The investigators wish to compare the brain distribution of GABA(A) receptors and GABA levels in young adult males with Fragile X Syndrome compared to idiopathic intellectual developmental disorder. The radiopharmaceutical \[18F\]flumazenil has been used to study GABA(A) receptor distribution in other genetic syndromes with autistic features; however, despite overwhelming evidence supporting the importance of the GABAergic system in FXS, no clinical investigation of this system in human FXS has been reported in the literature. Therefore, this study will provide the first in vivo comprehensive examination of the GABAergic system in FXS using hybrid positron emission tomography/ magnetic resonance imaging (PET/MRI).

Primary Outcome

Binding potential provides an estimate of the GABA (A) receptor distribution and affinity of \[18F\]flumazenil-PET to the GABA receptors. Binding potential will be measured in patients with fragile X syndrome and control group comprising individuals with idiopathic intellectual developmental disorder. Using imaging data obtained from PET that was corrected for attenuation and partial volume effects by MRI, nuclear medicine physicians will draw regions of interest (ROI's) around the areas of the

Interventions

  • DRUG [18F]flumazenil

Trial Details

FieldValue
Enrollment Target 17 participants
Start Date 2016-11-01
Est. Completion 2018-12-06
Phase Phase 1
Stanford University

1,744 total trials

Why NCT04308954 stopped before completion

NCT04308954 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 17 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (72% lower).

The record links to 0 conditions, and to 1 intervention - of which [18F]flumazenil is the first listed.

NCT04308954 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT04308954 about?

NCT04308954 is a clinical study titled "Neuroimaging GABA Physiology in Fragile X Syndrome". The investigators wish to compare the brain distribution of GABA(A) receptors and GABA levels in young adult males with Fragile X Syndrome compared to idiopathic intellectual developmental disorder. The radiopharmaceutical \[18F\]flumazenil has been used to study GABA(A) receptor distribution in oth...

What is the current status of trial NCT04308954?

This trial is currently terminated. It is a Phase 1 study. The enrollment target is 17 participants. The study started on 2016-11-01. Estimated completion is 2018-12-06.

What interventions are being tested in trial NCT04308954?

The interventions under investigation include: [18F]flumazenil (DRUG).

Who is sponsoring clinical trial NCT04308954?

This trial is sponsored by Stanford University, which has 1,744 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT04308954's enrollment target sits among peer trials

17 1785th of 2000 higher than 215 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

Nationwide trials with similar profiles

Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.

Similar enrollment target

  • NCT02090140 · 17 participants · NA

    Microfracture Versus Adipose Derived Stem Cells for the Treatment of Articular Cartilage Defects

  • NCT03317860 · 17 participants · NA

    Improving Measurement and Treatment of Post-stroke Neglect

  • NCT04356469 · 17 participants · Phase 2

    TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children

  • NCT04414046 · 17 participants · Phase 2

    TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Primary Immunodeficiency and Inherited Metabolic Disorders in Children

Similar registry start date

  • NCT05962346 · started 2026-12 · NA

    Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

  • NCT07125183 · started 2026-12 · Phase 2

    Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

  • NCT07292298 · started 2026-11 · Phase 2

    Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates

  • NCT04263285 · started 2026-10 · NA

    Treatment of Depression Post-SCI

Source: ClinicalTrials.gov NCT04308954, the US trial registry maintained by the National Library of Medicine. NCT04308954 (small enrollment · none site footprint · terminated) retrieved and formatted by PlainTrial, see methodology.