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NCT04281537 · ClinicalTrials.gov registry record
A Study to Describe the Experience of Both Patients and Their Clinicians in the Treatment of Fabry Disease With Enzyme Replacement Therapy.
A clinical trial, sponsored by Amicus Therapeutics.
- Completed
- Registry status
- 82
- Enrollment target
NCT04281537 is a clinical trial that has completed, run by Amicus Therapeutics. The registered enrollment target is 82 participants.
The verdict
NCT04281537 has completed, sponsored by Amicus Therapeutics.
- COMPLETED
- Registry status
- 82 participants
- Enrollment target
Study Summary
This is an international, non-interventional research study of adult patients with Fabry Disease and their caregivers. The study comprised a prospective time and motion evaluation and a cross-sectional evaluation of patient and caregiver-reported outcomes. The study evaluated the time associated with the preparation and administration of a single dose of enzyme replacement therapy (ERT) in patients by health care providers as well as the impact on Fabry patients and caregivers time and costs associated with an ERT treatment. The study also evaluated the patients' quality of life wellbeing, fatigue and work productivity.
Interventions
- DRUG Enzyme Replacement Therapy (ERT)
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 82 participants |
| Start Date | 2020-03-01 |
| Est. Completion | 2022-05-18 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT04281537
The ClinicalTrials.gov registry entry for NCT04281537 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 82 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Amicus Therapeutics, which has 34 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 1 intervention - of which Enzyme Replacement Therapy (ERT) is the first listed.
NCT04281537 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT04281537 about?
NCT04281537 is a clinical study titled "A Study to Describe the Experience of Both Patients and Their Clinicians in the Treatment of Fabry Disease With Enzyme Replacement Therapy.". This is an international, non-interventional research study of adult patients with Fabry Disease and their caregivers. The study comprised a prospective time and motion evaluation and a cross-sectional evaluation of patient and caregiver-reported outcomes. The study evaluated the time associated wit...
What is the current status of trial NCT04281537?
This trial is currently completed. The enrollment target is 82 participants. The study started on 2020-03-01. Estimated completion is 2022-05-18.
What interventions are being tested in trial NCT04281537?
The interventions under investigation include: Enzyme Replacement Therapy (ERT) (DRUG).
Who is sponsoring clinical trial NCT04281537?
This trial is sponsored by Amicus Therapeutics, which has 34 total clinical trials registered on ClinicalTrials.gov.
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