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NCT04227600 · ClinicalTrials.gov registry record · Phase 1
A Study of JR-171 in Patients With Mucopolysaccharidosis I
A Phase 1 study, sponsored by JCR Pharmaceuticals Co..
- Completed
- Registry status
- Phase 1
- Development phase
- 18
- Enrollment target
NCT04227600: Completed Phase 1 study, sponsored by JCR Pharmaceuticals Co..
NCT04227600 is a Phase 1 study that has completed, run by JCR Pharmaceuticals Co.. The registered enrollment target is 18 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (70% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04227600, a Phase 1 study, has completed, sponsored by JCR Pharmaceuticals Co..
- COMPLETED
- Registry status
- Phase 1
- Development phase
- 18 participants
- Enrollment target
Study Summary
Phase I/II, open-label, multicenter, multinational (Japan, Brazil and US),designed to evaluate the safety, pharmacokinetics and explore the efficacy for the treatment of mucopolysaccharidosis type I (MPS I).
Interventions
- DRUG JR-171 (lepunafusp alfa)
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 18 participants |
| Start Date | 2020-09-01 |
| Est. Completion | 2022-08-02 |
| Phase | Phase 1 |
What the finished NCT04227600 record still lists
NCT04227600 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 18 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (70% lower).
The record links to 0 conditions, and to 1 intervention - of which JR-171 (lepunafusp alfa) is the first listed.
NCT04227600 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT04227600 about?
NCT04227600 is a clinical study titled "A Study of JR-171 in Patients With Mucopolysaccharidosis I". Phase I/II, open-label, multicenter, multinational (Japan, Brazil and US),designed to evaluate the safety, pharmacokinetics and explore the efficacy for the treatment of mucopolysaccharidosis type I (MPS I).
What is the current status of trial NCT04227600?
This trial is currently completed. It is a Phase 1 study. The enrollment target is 18 participants. The study started on 2020-09-01. Estimated completion is 2022-08-02.
What interventions are being tested in trial NCT04227600?
The interventions under investigation include: JR-171 (lepunafusp alfa) (DRUG).
Who is sponsoring clinical trial NCT04227600?
This trial is sponsored by JCR Pharmaceuticals Co., which has 5 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT04227600's enrollment target sits among peer trials
18 1720th of 2000 higher than 216 of 2,000 other Phase 1 trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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