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NCT04199000 · ClinicalTrials.gov registry record
Clinical and Basic Investigations Into Congenital Disorders of Glycosylation
A clinical trial of Congenital Disorders of Glycosylation, sponsored by Icahn School of Medicine at Mount Sinai.
- Recruiting
- Registry status
- 500
- Enrollment target
- 12
- Study locations
NCT04199000: Recruiting study of Congenital Disorders of Glycosylation, sponsored by Icahn School of Medicine at Mount Sinai.
NCT04199000 is a study of Congenital Disorders of Glycosylation that is actively recruiting participants, run by Icahn School of Medicine at Mount Sinai. The registered enrollment target is 500 participants. The trial reports 12 study locations across 10 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04199000, a study of Congenital Disorders of Glycosylation, is actively recruiting participants, sponsored by Icahn School of Medicine at Mount Sinai.
- RECRUITING
- Registry status
- 500 participants
- Enrollment target
- 12
- Study locations
Study Summary
The purpose of this research is to study the natural history of congenital disorders of glycosylation and its causes and treatments.
Primary Outcome
Establish the prevalence and severity of specific morbid indicators of disease severity through use of the Nijmegen Progression CDG rating scale.
Conditions Studied
Study Locations (12)
Minnesota
- University of Minnesota - Minneapolis
- Mayo Clinic in Rochester - Rochester
Pennsylvania
- Children's Hospital of Philadelphia - Philadelphia
- Children's Hospital of Pittsburgh - Pittsburgh
California
- Rady Children's Hospital - San Diego
Colorado
- Children's Hospital of Colorado - Aurora
Florida
- Mayo Clinic Florida - Jacksonville
Louisiana
- Tulane University School of Medicine - New Orleans
Massachusetts
- Boston Children's Hospital - Boston
New York
- Icahn School of Medicine at Mount Sinai - New York
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 500 participants |
| Start Date | 2019-10-08 |
| Est. Completion | 2030-07-31 |
What NCT04199000 shows while recruiting
NCT04199000 is an observational study that tracks outcomes without assigning an intervention. The registered 500 participants enrollment target is mid-sized for trials with a published cap.
The record links to 1 condition, with Congenital Disorders of Glycosylation appearing as the primary indexed condition, and to 0 interventions.
NCT04199000 lists 12 locations in 10 states (Minnesota, Pennsylvania, California).
Frequently Asked Questions
What is clinical trial NCT04199000 about?
NCT04199000 is a clinical study titled "Clinical and Basic Investigations Into Congenital Disorders of Glycosylation". The purpose of this research is to study the natural history of congenital disorders of glycosylation and its causes and treatments.
What is the current status of trial NCT04199000?
This trial is currently recruiting. The enrollment target is 500 participants. The study started on 2019-10-08. Estimated completion is 2030-07-31.
What conditions does trial NCT04199000 study?
This clinical trial studies the following conditions: Congenital Disorders of Glycosylation.
Who is sponsoring clinical trial NCT04199000?
This trial is sponsored by Icahn School of Medicine at Mount Sinai, which has 708 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04199000 being conducted?
This trial has 12 study locations across California, Colorado, Florida, Louisiana, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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