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NCT04126005 · ClinicalTrials.gov registry record
Natural History Study of Patients With Canavan Disease (CANinform Study)
A clinical trial of Canavan Disease, sponsored by Aspa Therapeutics.
- Active
- Registry status
- 70
- Enrollment target
- 3
- Study locations
NCT04126005: Active study of Canavan Disease, sponsored by Aspa Therapeutics.
NCT04126005 is a study of Canavan Disease that is active but no longer recruiting, run by Aspa Therapeutics. The registered enrollment target is 70 participants. The trial reports 3 study locations across 3 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04126005, a study of Canavan Disease, is active but no longer recruiting, sponsored by Aspa Therapeutics.
- ACTIVE NOT RECRUITING
- Registry status
- 70 participants
- Enrollment target
- 3
- Study locations
Study Summary
This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural history of Canavan disease in children.
Primary Outcome
To enhance the understanding of the natural history of Canavan disease through retrospective data collection from patient medical records and prospective data collection from living patients, including: phenotypic characteristics and variability, genotype characteristics and variability, and disease progression and natural history.
Conditions Studied
Study Locations (3)
California
- UCSF Benioff Children's Hospital Oakland - Oakland
Massachusetts
- Massachusetts General Hospital - Boston
Other
- University Medical Center Hamburg-Eppendorf - Hamburg
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 70 participants |
| Start Date | 2019-10-10 |
| Est. Completion | 2025-07-31 |
What the registry record for NCT04126005 still lists
NCT04126005 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 70 participants, a relatively small participant target.
The record links to 1 condition, with Canavan Disease appearing as the primary indexed condition, and to 0 interventions.
NCT04126005 reports a single indexed study location in California, Massachusetts, Other.
Frequently Asked Questions
What is clinical trial NCT04126005 about?
NCT04126005 is a clinical study titled "Natural History Study of Patients With Canavan Disease (CANinform Study)". This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural history of Canavan disease in children.
What is the current status of trial NCT04126005?
This trial is currently active not recruiting. The enrollment target is 70 participants. The study started on 2019-10-10. Estimated completion is 2025-07-31.
What conditions does trial NCT04126005 study?
This clinical trial studies the following conditions: Canavan Disease.
Who is sponsoring clinical trial NCT04126005?
This trial is sponsored by Aspa Therapeutics, which has 2 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04126005 being conducted?
This trial has 3 study locations across California, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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