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NCT03945292 · ClinicalTrials.gov registry record · Phase 2

Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT)

A Phase 2 study, sponsored by Arrowhead Pharmaceuticals.

Completed
Registry status
Phase 2
Development phase
40
Enrollment target

NCT03945292: Completed Phase 2 study, sponsored by Arrowhead Pharmaceuticals.

NCT03945292 is a Phase 2 study that has completed, run by Arrowhead Pharmaceuticals. The registered enrollment target is 40 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (70% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT03945292, a Phase 2 study, has completed, sponsored by Arrowhead Pharmaceuticals.

COMPLETED
Registry status
Phase 2
Development phase
40 participants
Enrollment target

Study Summary

The purpose of AROAAT2001 (SEQUOIA) is to evaluate the safety, efficacy and tolerability of multiple doses of the investigational product, Fazirsiran Injection, administered subcutaneously to participants with alpha-1 antitrypsin deficiency (AATD).

Interventions

  • OTHER Placebo
  • DRUG Fazisiran Injection

Trial Details

FieldValue
Enrollment Target 40 participants
Start Date 2019-08-07
Est. Completion 2023-09-18
Phase Phase 2
Arrowhead Pharmaceuticals

15 total trials

What the finished NCT03945292 record still lists

NCT03945292 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 40 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (70% lower).

The record links to 0 conditions, and to 2 interventions - of which Placebo is the first listed.

NCT03945292 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT03945292 about?

NCT03945292 is a clinical study titled "Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT)". The purpose of AROAAT2001 (SEQUOIA) is to evaluate the safety, efficacy and tolerability of multiple doses of the investigational product, Fazirsiran Injection, administered subcutaneously to participants with alpha-1 antitrypsin deficiency (AATD).

What is the current status of trial NCT03945292?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 40 participants. The study started on 2019-08-07. Estimated completion is 2023-09-18.

What interventions are being tested in trial NCT03945292?

The interventions under investigation include: Placebo (OTHER), Fazisiran Injection (DRUG).

Who is sponsoring clinical trial NCT03945292?

This trial is sponsored by Arrowhead Pharmaceuticals, which has 15 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT03945292's enrollment target sits among peer trials

40 1362nd of 2000 higher than 542 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT03945292, the US trial registry maintained by the National Library of Medicine. NCT03945292 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.