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NCT03759379 · ClinicalTrials.gov registry record · Phase 3

HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)

A Phase 3 study, sponsored by Alnylam Pharmaceuticals.

Completed
Registry status
Phase 3
Development phase
164
Enrollment target

NCT03759379 is a Phase 3 study that has completed, run by Alnylam Pharmaceuticals. The registered enrollment target is 164 participants.

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The verdict

NCT03759379, a Phase 3 study, has completed, sponsored by Alnylam Pharmaceuticals.

COMPLETED
Registry status
Phase 3
Development phase
164 participants
Enrollment target

Study Summary

The purpose of this study is to evaluate the efficacy and safety of vutrisiran (ALN-TTRSC02) in participants with hereditary transthyretin amyloidosis (hATTR amyloidosis). Participants will receive vutrisiran subcutaneous (SC) injection once every 3 months (q3M) or the reference comparator patisiran intravenous (IV) injection once every 3 weeks (q3w) during the 18 month Treatment Period. This study will use the placebo arm of the APOLLO study (NCT01960348) as an external comparator for the primary and most other efficacy endpoints during the 18 Month Treatment Period. Following the 18 Month Treatment Period, all participants will be randomized to receive vutrisiran 50 mg SC injection once every 6 months (q6M) or vutrisiran 25 mg q3M in the Randomized Treatment Extension (RTE) Period. Upon implementation of Amendment 6, participants receiving vutrisiran SC 50 mg q6M will transition to vutrisiran SC 25 mg q3M at their next scheduled dosing.

Interventions

  • DRUG Vutrisiran
  • DRUG Patisiran

Trial Details

FieldValue
Enrollment Target 164 participants
Start Date 2019-02-14
Est. Completion 2025-11-05
Phase Phase 3

Sponsor

Alnylam Pharmaceuticals

49 total trials

What the Registry Record Tells You About NCT03759379

The ClinicalTrials.gov registry entry for NCT03759379 describes a study currently listed as completed, categorized as Phase 3. The registered enrollment target is 164 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Alnylam Pharmaceuticals, which has 49 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 2 interventions - of which Vutrisiran is the first listed.

NCT03759379 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT03759379 about?

NCT03759379 is a clinical study titled "HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)". The purpose of this study is to evaluate the efficacy and safety of vutrisiran (ALN-TTRSC02) in participants with hereditary transthyretin amyloidosis (hATTR amyloidosis). Participants will receive vutrisiran subcutaneous (SC) injection once every 3 months (q3M) or the reference comparator patisiran...

What is the current status of trial NCT03759379?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 164 participants. The study started on 2019-02-14. Estimated completion is 2025-11-05.

What interventions are being tested in trial NCT03759379?

The interventions under investigation include: Vutrisiran (DRUG), Patisiran (DRUG).

Who is sponsoring clinical trial NCT03759379?

This trial is sponsored by Alnylam Pharmaceuticals, which has 49 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.