Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT03587116 · ClinicalTrials.gov registry record · Phase 3

A Study to Evaluate Prospective Efficacy and Safety Data of Current FIX Prophylaxis Replacement Therapy in Adult Hemophilia B Subjects (FIX:C≤2%) or Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Subjects (FVIII:C≤1%)

A Phase 3 study, sponsored by Pfizer.

Completed
Registry status
Phase 3
Development phase
212
Enrollment target

NCT03587116: Completed Phase 3 study, sponsored by Pfizer.

NCT03587116 is a Phase 3 study that has completed, run by Pfizer. The registered enrollment target is 212 participants, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (73% lower). According to ClinicalTrials.gov, the official US trial registry.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT03587116, a Phase 3 study, has completed, sponsored by Pfizer.

COMPLETED
Registry status
Phase 3
Development phase
212 participants
Enrollment target

Study Summary

To establish baseline prospective efficacy data of current FIX prophylaxis replacement therapy in the usual care setting of hemophilia B subjects, who are negative for nAb to AAV-Spark100, prior to the Phase 3 gene therapy study. To establish baseline prospective efficacy data of current FVIII prophylaxis replacement therapy in the usual care setting of hemophilia A subjects, who are negative for nAb to AAV6, prior to the Phase 3 gene therapy study. The enrollment for hemophilia A participants is completed. At this time participants are only being enrolled for hemophilia B cohort.

Primary Outcome

ABR per participant was calculated as number of bleeds over number of days from baseline visit (Day 1 of the study) to end of study multiplication(\*)365.25 days. All bleeds included treated and untreated bleeds. A treated bleed was defined as an event necessitating administration of coagulation factor within 72 hours of signs or symptoms of bleeding. An untreated bleed was defined as an event not necessitating administration of coagulation factor within 72 hours of signs or symptoms of bleeding

Interventions

  • DRUG Standard of Care FVIII Replacement therapy
  • DRUG Standard of Care FIX Replacement therapy

Trial Details

FieldValue
Enrollment Target 212 participants
Start Date 2018-07-26
Est. Completion 2024-12-13
Phase Phase 3
Pfizer

1,845 total trials

What the finished NCT03587116 record still lists

NCT03587116 is an interventional study that assigns participants to a tested intervention. The registered 212 participants enrollment target is mid-sized for trials with a published cap, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (73% lower).

The record links to 0 conditions, and to 2 interventions - of which Standard of Care FVIII Replacement therapy is the first listed.

NCT03587116 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT03587116 about?

NCT03587116 is a clinical study titled "A Study to Evaluate Prospective Efficacy and Safety Data of Current FIX Prophylaxis Replacement Therapy in Adult Hemophilia B Subjects (FIX:C≤2%) or Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Subjects (FVIII:C≤1%)". To establish baseline prospective efficacy data of current FIX prophylaxis replacement therapy in the usual care setting of hemophilia B subjects, who are negative for nAb to AAV-Spark100, prior to the Phase 3 gene therapy study. To establish baseline prospective efficacy data of current FVIII prop...

What is the current status of trial NCT03587116?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 212 participants. The study started on 2018-07-26. Estimated completion is 2024-12-13.

What interventions are being tested in trial NCT03587116?

The interventions under investigation include: Standard of Care FVIII Replacement therapy (DRUG), Standard of Care FIX Replacement therapy (DRUG).

Who is sponsoring clinical trial NCT03587116?

This trial is sponsored by Pfizer, which has 1,845 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT03587116's enrollment target sits among peer trials

212 1335th of 2000 higher than 664 of 2,000 other Phase 3 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 3 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

Nationwide trials with similar profiles

Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.

Similar enrollment target

  • NCT04228978 · 212 participants · NA

    Promote Weight Loss in Obese Peripheral Artery Disease (PAD) Patients to Prevent Mobility Loss

  • NCT04725721 · 212 participants · NA

    Testing FIRST in Youth Outpatient Psychotherapy

  • NCT06257576 · 212 participants · Phase 3

    Function of Tamsulosin in Older Males Undergoing Surgery with Indwelling Catheter

  • NCT06456593 · 212 participants · Phase 2

    Efficacy and Safety of Obefazimod in Subjects With Moderately to Severely Active Crohn's Disease

Similar registry start date

  • NCT05962346 · started 2026-12 · NA

    Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

  • NCT07125183 · started 2026-12 · Phase 2

    Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

  • NCT07292298 · started 2026-11 · Phase 2

    Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates

  • NCT04263285 · started 2026-10 · NA

    Treatment of Depression Post-SCI

Source: ClinicalTrials.gov NCT03587116, the US trial registry maintained by the National Library of Medicine. NCT03587116 (mid enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.