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NCT03315182 · ClinicalTrials.gov registry record · Phase 1
Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB
A Phase 1 study, sponsored by Abeona Therapeutics.
- Terminated
- Registry status
- Phase 1
- Development phase
- 11
- Enrollment target
NCT03315182: Clinical Trial Phase 1 study, sponsored by Abeona Therapeutics.
NCT03315182 is a Phase 1 study that was terminated before completion, run by Abeona Therapeutics. The registered enrollment target is 11 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (82% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT03315182, a Phase 1 study, was terminated before completion, sponsored by Abeona Therapeutics.
- TERMINATED
- Registry status
- Phase 1
- Development phase
- 11 participants
- Enrollment target
Study Summary
Open-label, dose-escalation clinical trial of rAAV9.CMV.hNAGLU injected intravenously through a peripheral limb vein
Interventions
- BIOLOGICAL rAAV9.CMV.hNAGLU
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 11 participants |
| Start Date | 2017-10-16 |
| Est. Completion | 2022-04-07 |
| Phase | Phase 1 |
Why NCT03315182 stopped before completion
NCT03315182 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 11 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (82% lower).
The record links to 0 conditions, and to 1 intervention - of which rAAV9.CMV.hNAGLU is the first listed.
NCT03315182 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT03315182 about?
NCT03315182 is a clinical study titled "Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB". Open-label, dose-escalation clinical trial of rAAV9.CMV.hNAGLU injected intravenously through a peripheral limb vein
What is the current status of trial NCT03315182?
This trial is currently terminated. It is a Phase 1 study. The enrollment target is 11 participants. The study started on 2017-10-16. Estimated completion is 2022-04-07.
What interventions are being tested in trial NCT03315182?
The interventions under investigation include: rAAV9.CMV.hNAGLU (BIOLOGICAL).
Who is sponsoring clinical trial NCT03315182?
This trial is sponsored by Abeona Therapeutics, which has 8 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT03315182's enrollment target sits among peer trials
11 1911th of 2000 higher than 88 of 2,000 other Phase 1 trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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