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NCT03256799 · ClinicalTrials.gov registry record · Phase 4

Evaluation of Ivacaftor in Patients Using Ataluren for Nonsense Mutations

A Phase 4 study of Cystic Fibrosis, sponsored by University of Alabama at Birmingham.

Completed
Registry status
Phase 4
Development phase
1
Enrollment target
1
Study location

NCT03256799: Completed Phase 4 study of Cystic Fibrosis, sponsored by University of Alabama at Birmingham.

NCT03256799 is a Phase 4 study of Cystic Fibrosis that has completed, run by University of Alabama at Birmingham. The registered enrollment target is 1 participants, below the 179-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target (99% lower). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT03256799, a Phase 4 study of Cystic Fibrosis, has completed, sponsored by University of Alabama at Birmingham.

COMPLETED
Registry status
Phase 4
Development phase
1 participants
Enrollment target
1
Study location

Study Summary

The purpose of this study is to explore the combination of Ataluren and ivacaftor as a treatment for patients with a specific cystic fibrosis mutation

Primary Outcome

change in lung function as measured by spirometry

Conditions Studied

Interventions

  • DRUG Ivacaftor/Ataluren

Study Locations (1)

Alabama

  • University of Alabama at Birmingham - Birmingham

Trial Details

FieldValue
Enrollment Target 1 participants
Start Date 2017-03-17
Est. Completion 2018-02-16
Phase Phase 4
University of Alabama at Birmingham

1,160 total trials

What the finished NCT03256799 record still lists

NCT03256799 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 1 participants, a relatively small participant target, below the 179-participant average among 169 other Cystic Fibrosis trials with a reported enrollment target (99% lower).

The record links to 1 condition, with Cystic Fibrosis appearing as the primary indexed condition, and to 1 intervention - of which Ivacaftor/Ataluren is the first listed.

NCT03256799 reports a single indexed study location in Alabama.

Frequently Asked Questions

What is clinical trial NCT03256799 about?

NCT03256799 is a clinical study titled "Evaluation of Ivacaftor in Patients Using Ataluren for Nonsense Mutations". The purpose of this study is to explore the combination of Ataluren and ivacaftor as a treatment for patients with a specific cystic fibrosis mutation

What is the current status of trial NCT03256799?

This trial is currently completed. It is a Phase 4 study. The enrollment target is 1 participants. The study started on 2017-03-17. Estimated completion is 2018-02-16.

What conditions does trial NCT03256799 study?

This clinical trial studies the following conditions: Cystic Fibrosis.

What interventions are being tested in trial NCT03256799?

The interventions under investigation include: Ivacaftor/Ataluren (DRUG).

Who is sponsoring clinical trial NCT03256799?

This trial is sponsored by University of Alabama at Birmingham, which has 1,160 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03256799 being conducted?

This trial has 1 study location across Alabama. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Cystic Fibrosis

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT03256799's enrollment target sits among peer trials

1 170th of 169 the lowest of 169 other Cystic Fibrosis trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Cystic Fibrosis trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT03256799, the US trial registry maintained by the National Library of Medicine. NCT03256799 (small enrollment · single site footprint · completed) retrieved and formatted by PlainTrial, see methodology.