Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT03173937 · ClinicalTrials.gov registry record · Phase 1

Unrelated Umbilical Cord Blood Transplantation for Severe Aplastic Anemia and Hypo-plastic MDS Using CordIn(TM), Umbilical Cord Blood-Derived Ex Vivo Expanded Stem and Progenitor Cells to Expedite Engraftment and Improve Transplant Outcome

A Phase 1 study of Myelodysplastic Syndrome (MDS) and Severe Aplastic Anemia, sponsored by National Heart, Lung, and Blood Institute (NHLBI).

Recruiting
Registry status
Phase 1
Development phase
37
Enrollment target
1
Study location

NCT03173937 is a Phase 1 study of Myelodysplastic Syndrome (MDS) and Severe Aplastic Anemia that is actively recruiting participants, run by National Heart, Lung, and Blood Institute (NHLBI). The registered enrollment target is 37 participants, below the 91-participant average among 17 other Myelodysplastic Syndrome (MDS) trials with a reported enrollment target (59% lower). The trial reports 1 study location across 1 state.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT03173937, a Phase 1 study of Myelodysplastic Syndrome (MDS) and Severe Aplastic Anemia, is actively recruiting participants, sponsored by National Heart, Lung, and Blood Institute (NHLBI).

RECRUITING
Registry status
Phase 1
Development phase
37 participants
Enrollment target
1
Study location

Study Summary

Background: Severe aplastic anemia (SAA) and myelodysplastic syndrome (MDS) are bone marrow diseases. People with these diseases usually need a bone marrow transplant. Researchers are testing ways to make stem cell transplant safer and more effective. Objective: To test if treating people with SAA or MDS with a co-infusion of blood stem cells from a family member and cord blood stem cells from an unrelated donor is safe and effective. Eligibility: Recipients ages 4-60 with SAA or MDS Donors ages 4-75 Design: Recipients will be screened with: * Blood, lung, and heart tests * Bone marrow biopsy * CT scan Recipients will have an IV line placed into a vein in the neck. Starting 11 days before the transplant they will have several chemotherapy infusions and 1 30-minute radiation dose. Recipients will get the donor cells through the IV line. They will stay in the hospital 3-4 weeks. After discharge, they will have visits: * First 3-4 months: 1-2 times weekly * Then every 6 months for 5 years Donors will be screened with: * Physical exam * Medical history * Blood tests Donors veins will be checked for suitability for stem cell collection. They may need an IV line to be placed in a thigh vein. Donors will get Filgrastim or biosimilar (G-CSF) injections daily for 5-7 days. On the last day, they will have apheresis: Blood drawn from one arm or leg runs through a machine and into the other arm or leg. This may be repeated 2 days or 2-4 weeks later.

Interventions

  • BIOLOGICAL Omidubicel (former CordIn)
  • DEVICE Miltenyi CliniMACS(R) CD34 Reagent System

Study Locations (1)

Maryland

  • National Institutes of Health Clinical Center - Bethesda

Trial Details

FieldValue
Enrollment Target 37 participants
Start Date 2017-06-13
Est. Completion 2032-03-01
Phase Phase 1

What the Registry Record Tells You About NCT03173937

The ClinicalTrials.gov registry entry for NCT03173937 describes a study currently listed as recruiting, categorized as Phase 1. The registered enrollment target is 37 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 91-participant average among 17 other Myelodysplastic Syndrome (MDS) trials with a reported enrollment target (59% lower). The listed sponsor is National Heart, Lung, and Blood Institute (NHLBI), which has 501 total studies on file at ClinicalTrials.gov.

The record links to 3 conditions, with Myelodysplastic Syndrome (MDS) appearing as the primary indexed condition, and to 2 interventions - of which Omidubicel (former CordIn) is the first listed.

NCT03173937 reports 1 study location spanning 1 distinct geographic area - top geographies include Maryland.

Frequently Asked Questions

What is clinical trial NCT03173937 about?

NCT03173937 is a clinical study titled "Unrelated Umbilical Cord Blood Transplantation for Severe Aplastic Anemia and Hypo-plastic MDS Using CordIn(TM), Umbilical Cord Blood-Derived Ex Vivo Expanded Stem and Progenitor Cells to Expedite Engraftment and Improve Transplant Outcome". Background: Severe aplastic anemia (SAA) and myelodysplastic syndrome (MDS) are bone marrow diseases. People with these diseases usually need a bone marrow transplant. Researchers are testing ways to make stem cell transplant safer and more effective. Objective: To test if treating people with SA...

What is the current status of trial NCT03173937?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 37 participants. The study started on 2017-06-13. Estimated completion is 2032-03-01.

What conditions does trial NCT03173937 study?

This clinical trial studies the following conditions: Myelodysplastic Syndrome (MDS), Severe Aplastic Anemia, Hypo-Plastic MDS.

What interventions are being tested in trial NCT03173937?

The interventions under investigation include: Omidubicel (former CordIn) (BIOLOGICAL), Miltenyi CliniMACS(R) CD34 Reagent System (DEVICE).

Who is sponsoring clinical trial NCT03173937?

This trial is sponsored by National Heart, Lung, and Blood Institute (NHLBI), which has 501 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03173937 being conducted?

This trial has 1 study location across Maryland. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Myelodysplastic Syndrome (MDS)

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.