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NCT03140969 · ClinicalTrials.gov registry record · Phase 1

Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene

A Phase 1 study, sponsored by Laboratoires Thea.

Completed
Registry status
Phase 1
Development phase
11
Enrollment target

NCT03140969: Completed Phase 1 study, sponsored by Laboratoires Thea.

NCT03140969 is a Phase 1 study that has completed, run by Laboratoires Thea. The registered enrollment target is 11 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (82% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT03140969, a Phase 1 study, has completed, sponsored by Laboratoires Thea.

COMPLETED
Registry status
Phase 1
Development phase
11 participants
Enrollment target

Study Summary

The purpose of this study is to evaluate the safety and tolerability of QR-110 administered via intravitreal injection in subjects with LCA due to the CEP290 p.Cys998X mutation.

Interventions

  • DRUG QR-110

Trial Details

FieldValue
Enrollment Target 11 participants
Start Date 2017-10-16
Est. Completion 2019-10-02
Phase Phase 1
Laboratoires Thea

11 total trials

What the finished NCT03140969 record still lists

NCT03140969 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 11 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (82% lower).

The record links to 0 conditions, and to 1 intervention - of which QR-110 is the first listed.

NCT03140969 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT03140969 about?

NCT03140969 is a clinical study titled "Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene". The purpose of this study is to evaluate the safety and tolerability of QR-110 administered via intravitreal injection in subjects with LCA due to the CEP290 p.Cys998X mutation.

What is the current status of trial NCT03140969?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 11 participants. The study started on 2017-10-16. Estimated completion is 2019-10-02.

What interventions are being tested in trial NCT03140969?

The interventions under investigation include: QR-110 (DRUG).

Who is sponsoring clinical trial NCT03140969?

This trial is sponsored by Laboratoires Thea, which has 11 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT03140969's enrollment target sits among peer trials

11 1911th of 2000 higher than 88 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT03140969, the US trial registry maintained by the National Library of Medicine. NCT03140969 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.