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NCT02724228 · ClinicalTrials.gov registry record · Phase 2

A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)

A Phase 2 study of Achondroplasia, sponsored by BioMarin Pharmaceutical.

Active
Registry status
Phase 2
Development phase
30
Enrollment target
9
Study locations

NCT02724228 is a Phase 2 study of Achondroplasia that is active but no longer recruiting, run by BioMarin Pharmaceutical. The registered enrollment target is 30 participants, below the 148-participant average among 9 other Achondroplasia trials with a reported enrollment target (80% lower). The trial reports 9 study locations across 7 states.

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The verdict

NCT02724228, a Phase 2 study of Achondroplasia, is active but no longer recruiting, sponsored by BioMarin Pharmaceutical.

ACTIVE NOT RECRUITING
Registry status
Phase 2
Development phase
30 participants
Enrollment target
9
Study locations

Study Summary

This is a Phase 2, Open-Label, Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of BMN 111 in Children with Achondroplasia. The primary objective is to evaluate the long-term safety and tolerability of daily SC injections of BMN 111 in children with ACH who have completed two years of treatment in the 111-202 study.

Conditions Studied

Interventions

  • DRUG BMN 111

Study Locations (9)

California

  • Children's Hospital & Research Center Oakland - Oakland
  • Harbor - UCLA Medical Center - Torrance

Other

  • Institut Necker - Paris
  • Guys & St. Thomas NHS Foundation Trust Evelina Hospital - London

Illinois

  • Ann and Robert H. Lurie Childrens Hospital of Chicago - Chicago

Maryland

  • Johns Hopkins McKusick - Institute of Genetic Medicine - Baltimore

Tennessee

  • Vanderbilt University - Nashville

Texas

  • Baylor College of Medicine - Houston

Victoria

  • Murdoch Children's Research Institute - Parkville

Trial Details

FieldValue
Enrollment Target 30 participants
Start Date 2016-01-26
Est. Completion 2028-02
Phase Phase 2

Sponsor

BioMarin Pharmaceutical

80 total trials

What the Registry Record Tells You About NCT02724228

The ClinicalTrials.gov registry entry for NCT02724228 describes a study currently listed as active not recruiting, categorized as Phase 2. The registered enrollment target is 30 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 148-participant average among 9 other Achondroplasia trials with a reported enrollment target (80% lower). The listed sponsor is BioMarin Pharmaceutical, which has 80 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Achondroplasia appearing as the primary indexed condition, and to 1 intervention - of which BMN 111 is the first listed.

NCT02724228 reports 9 study locations spanning 7 distinct geographic areas - top geographies include California, Other, Illinois.

Frequently Asked Questions

What is clinical trial NCT02724228 about?

NCT02724228 is a clinical study titled "A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)". This is a Phase 2, Open-Label, Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of BMN 111 in Children with Achondroplasia. The primary objective is to evaluate the long-term safety and tolerability of daily SC injections of BMN 111 in children with ACH who have completed...

What is the current status of trial NCT02724228?

This trial is currently active not recruiting. It is a Phase 2 study. The enrollment target is 30 participants. The study started on 2016-01-26. Estimated completion is 2028-02.

What conditions does trial NCT02724228 study?

This clinical trial studies the following conditions: Achondroplasia.

What interventions are being tested in trial NCT02724228?

The interventions under investigation include: BMN 111 (DRUG).

Who is sponsoring clinical trial NCT02724228?

This trial is sponsored by BioMarin Pharmaceutical, which has 80 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT02724228 being conducted?

This trial has 9 study locations across California, Illinois, Maryland, Tennessee, Texas. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.