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NCT01027884 · ClinicalTrials.gov registry record · Phase 3

Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)

A Phase 3 study of Muscular Dystrophy, Duchenne and Ambulatory Care, sponsored by Santhera Pharmaceuticals.

Completed
Registry status
Phase 3
Development phase
65
Enrollment target
20
Study locations

NCT01027884: Completed Phase 3 study of Muscular Dystrophy, Duchenne and Ambulatory Care, sponsored by Santhera Pharmaceuticals.

NCT01027884 is a Phase 3 study of Muscular Dystrophy, Duchenne and Ambulatory Care that has completed, run by Santhera Pharmaceuticals. The registered enrollment target is 65 participants, below the 91-participant average among 4 other Muscular Dystrophy, Duchenne trials with a reported enrollment target (29% lower). The trial reports 20 study locations across 10 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT01027884, a Phase 3 study of Muscular Dystrophy, Duchenne and Ambulatory Care, has completed, sponsored by Santhera Pharmaceuticals.

COMPLETED
Registry status
Phase 3
Development phase
65 participants
Enrollment target
20
Study locations

Study Summary

The aim of this Phase III study was to assess the efficacy of idebenone on pulmonary function, motor function, muscle strength and quality of life in patients with DMD. Furthermore, the safety and tolerability of idebenone was assessed.

Primary Outcome

Change from Baseline in Percent Predicted Peak Expiratory Flow (PEF) at Week 52

Interventions

  • DRUG Placebo
  • DRUG Idebenone

Study Locations (20)

Other

  • Dr. Günther Bernert, Prim. Univ. Doz. - Vienna
  • University Hospitals Leuven- Children Hospital - Leuven
  • Hôpital Roger Salengro, CHRU Lille - Lille
  • Prof. Thomas Voit , MD, PhD - Paris
  • Universitätsklinikum Essen, Zentrum für Kinderheikunde - Essen
  • Universitätsklinik Freiburg Zentrum für Kinderheilkunde und Jugendmedizin - Freiburg im Breisgau
  • Fondazione IRCCS "Eugenio Medea" - Bosisio Parini, Lecco
  • Azienda Ospedaliera Niguarda Ca' Granda Centro Clinico Nemo - Milan
  • Azienda Ospedaliera Universitaria della Seconda Università degli Studi di Napoli - Naples
  • Hospital Universitario 12 de Octubre - Madrid

Texas

  • University of Texas Southwestern Medical Center - Dallas
  • Methodist Neurological Institute - Houston

California

  • University of California Davis Medical Center - Sacramento

Colorado

  • Children's Hospital Colorado - Aurora

Florida

  • University of Florida - Gainesville

North Carolina

  • Carolinas Medical Center, Neurosciences and Spine Institute - Charlotte

Pennsylvania

  • The Children's Hospital of Philadelphia - Philadelphia

Tennessee

  • Monroe Carell, Jr. Children's Hospital at Vanderbilt - Nashville

Trial Details

FieldValue
Enrollment Target 65 participants
Start Date 2009-07
Est. Completion 2014-04
Phase Phase 3
Santhera Pharmaceuticals

7 total trials

What the finished NCT01027884 record still lists

NCT01027884 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 65 participants, a relatively small participant target, below the 91-participant average among 4 other Muscular Dystrophy, Duchenne trials with a reported enrollment target (29% lower).

The record links to 2 conditions, with Muscular Dystrophy, Duchenne appearing as the primary indexed condition, and to 2 interventions - of which Placebo is the first listed.

NCT01027884 names 20 study sites across 10 states, led by Other, Texas, California.

Frequently Asked Questions

What is clinical trial NCT01027884 about?

NCT01027884 is a clinical study titled "Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)". The aim of this Phase III study was to assess the efficacy of idebenone on pulmonary function, motor function, muscle strength and quality of life in patients with DMD. Furthermore, the safety and tolerability of idebenone was assessed.

What is the current status of trial NCT01027884?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 65 participants. The study started on 2009-07. Estimated completion is 2014-04.

What conditions does trial NCT01027884 study?

This clinical trial studies the following conditions: Muscular Dystrophy, Duchenne, Ambulatory Care.

What interventions are being tested in trial NCT01027884?

The interventions under investigation include: Placebo (DRUG), Idebenone (DRUG).

Who is sponsoring clinical trial NCT01027884?

This trial is sponsored by Santhera Pharmaceuticals, which has 7 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT01027884 being conducted?

This trial has 20 study locations across California, Colorado, Florida, North Carolina, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Source: ClinicalTrials.gov NCT01027884, the US trial registry maintained by the National Library of Medicine. NCT01027884 (small enrollment · wide site footprint · completed) retrieved and formatted by PlainTrial, see methodology.