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NCT00001521 · ClinicalTrials.gov registry record · Phase 3

Three Drug Combination Therapy Versus Conventional Treatment of Children With Congenital Adrenal Hyperplasia

A Phase 3 study, sponsored by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD).

Completed
Registry status
Phase 3
Development phase
66
Enrollment target

NCT00001521: Completed Phase 3 study, sponsored by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD).

NCT00001521 is a Phase 3 study that has completed, run by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD). The registered enrollment target is 66 participants, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (91% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT00001521, a Phase 3 study, has completed, sponsored by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD).

COMPLETED
Registry status
Phase 3
Development phase
66 participants
Enrollment target

Study Summary

This study was developed to determine if a combination of four drugs (flutamide, testolactone, reduced hydrocortisone dose, and fludrocortisone) can normalize growth in children with congenital adrenal hyperplasia. The study will take 60 children, boys and girls, and divide them into 2 groups based on the medications given. Group one will receive the new four-drug combination. Group two will receive the standard treatment for congenital adrenal hyperplasia (hydrocortisone and fludrocortisone). The boys in group one will take the medication until the age of 14 at which time they will stop taking the four-drug combination and begin receiving the standard treatment for congenital adrenal hyperplasia. Girls in group one will take the four-drug combination until the age of 13, at which time they will stop and begin receiving the standard treatment for congenital adrenal hyperplasia plus flutamide. Flutamide will be given to the girls until two years after their first menstrual period or until adult height. All of the children will be followed until they reach their final adult height. The effectiveness of the treatment will be determined by measuring the patient's adult height.

Primary Outcome

Adult height expressed in standard deviation score (SDS) units relative to the general population, with attainment of adult height defined as incremental growth \< 1.5 cm over 12 months. Adult height SDS was based on National Health and Nutrition Examination Survey (Centers for Disease Control and Prevention, National Center for Health Statistics) data at 20 years old.

Interventions

  • DRUG Letrozole
  • DRUG Flutamide
  • DRUG Hydrocortisone
  • DRUG Fludrocortisone
  • DRUG Testolactone

Trial Details

FieldValue
Enrollment Target 66 participants
Start Date 1995-06-08
Est. Completion 2024-04-01
Phase Phase 3

What the finished NCT00001521 record still lists

NCT00001521 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 66 participants, a relatively small participant target, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (91% lower).

The record links to 0 conditions, and to 5 interventions - of which Letrozole is the first listed.

NCT00001521 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT00001521 about?

NCT00001521 is a clinical study titled "Three Drug Combination Therapy Versus Conventional Treatment of Children With Congenital Adrenal Hyperplasia". This study was developed to determine if a combination of four drugs (flutamide, testolactone, reduced hydrocortisone dose, and fludrocortisone) can normalize growth in children with congenital adrenal hyperplasia. The study will take 60 children, boys and girls, and divide them into 2 groups based...

What is the current status of trial NCT00001521?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 66 participants. The study started on 1995-06-08. Estimated completion is 2024-04-01.

What interventions are being tested in trial NCT00001521?

The interventions under investigation include: Letrozole (DRUG), Flutamide (DRUG), Hydrocortisone (DRUG), Fludrocortisone (DRUG), Testolactone (DRUG).

Who is sponsoring clinical trial NCT00001521?

This trial is sponsored by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), which has 305 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT00001521's enrollment target sits among peer trials

66 1797th of 2000 higher than 204 of 2,000 other Phase 3 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 3 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT00001521, the US trial registry maintained by the National Library of Medicine. NCT00001521 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.