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Friedreich's Ataxia clinical trials
2 of 6 indexed Friedreich's Ataxia trials are currently recruiting.
6 US clinical trials · 2 currently recruiting
Friedreich's Ataxia is the subject of 6 registered US clinical trials on ClinicalTrials.gov, 2 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 3 in Phase 1-2 (earlier-stage). The most active sponsor is University of South Florida, running 2 of these trials.
The research picture
Friedreich's Ataxia has 6 registered US clinical trials, 2 of them open to new participants right now, about 33% of the total.
- 2
- recruiting participants now
- 33%
- of trials open to enrollment
- 0
- in Phase 3–4 (later-stage)
- 2
- top sponsor: University of South Florida
Active & Recent Trials
6 total, page 1 of 1
Biomarkers in Friedreich's Ataxia
University of Florida
NCT02497534
Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)
Weill Medical College of Cornell University
NCT02316314
Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia
Shire
NCT01898884
Preliminary Study of the Scale To Assess Ataxia and Neurologic Dysfunction (STAND)
University of South Florida
NCT02179333
A First in Human Study of RT001 in Patients With Friedreich's Ataxia
Biojiva
NCT02445794
EPI-743 in Friedreich's Ataxia Point Mutations
University of South Florida
NCT01962363
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 1 | 2 |
| Phase 2 | 1 |
Top Sponsors
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Reading the Friedreich's Ataxia Trial Landscape
6 indexed Friedreich's Ataxia studies · 2 recruiting (33%).
Phase mix: 0 late (III/IV) vs 3 early (I/II).
Top sponsor: University of South Florida (2 trials), 4 others listed. 6 shown below, recruiting first.
How to read this condition's trial landscape
That ratio is a useful proxy for activity level: a high share of recruiting studies often signals that research interest is current and that new enrollment opportunities are appearing, while a low share typically means the field is dominated by completed or follow-up work where most participant spots have already been filled. These counts reflect the public registry only and include studies at every stage of design, so they should be read as an index of research attention rather than as a measure of treatment availability.
Phase 1 and Phase 2 studies focus on early safety signals, dosing, and preliminary effect, while Phase 3 studies are typically the larger efficacy and safety trials submitted toward regulatory review, and Phase 4 studies follow approved interventions in real-world use. A condition weighted toward later phases often reflects a mature research pipeline with several interventions already close to or past approval, whereas a heavier early-phase tilt suggests the field is still exploring new mechanisms and candidate approaches.
All figures are derived from the public ClinicalTrials.gov dataset maintained by the National Library of Medicine and are reproduced here for reference. Inclusion of a trial, sponsor, or intervention on this page is neither an endorsement nor a recommendation, eligibility, protocol changes, and site-level status can shift frequently, so always verify current details on ClinicalTrials.gov and consult a qualified healthcare provider before acting on anything you see here.
Frequently Asked Questions
How many clinical trials are there for Friedreich's Ataxia?
PlainTrial tracks 6 US clinical trials for Friedreich's Ataxia, of which 2 are currently recruiting participants. Data sourced from ClinicalTrials.gov.
How do I find a recruiting trial for Friedreich's Ataxia?
Use the trial list above filtered by "Recruiting" status, or visit our trial finder at /recruiting to search by condition and state. Always discuss trial participation with your healthcare provider before enrolling.
Is this data current?
Data is sourced from ClinicalTrials.gov and reflects our most recent data pull. Trial status may have changed since then. Always verify current information at ClinicalTrials.gov before making decisions about participation.
Related
Disclaimer: This information is provided for informational purposes only and does not constitute professional advice. Data is sourced from ClinicalTrials.gov (National Library of Medicine). Consult a qualified professional before making decisions based on this data.
Read our methodology - how this data is sourced, computed, and verified.
Source: ClinicalTrials.gov (NIH/NLM) ClinicalTrials.gov AACT registry · 2026 Trial counts and statuses sourced from ClinicalTrials.gov. Sponsor counts include both industry and federal/academic sponsors.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page aggregates every registered trial for this condition, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.