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NCT07588581 · ClinicalTrials.gov registry record · Phase 1
Personalized Antisense Oligonucleotide for A Single Participant With UBTF Gene Mutation
A Phase 1 study, sponsored by n-Lorem Foundation.
- Active
- Registry status
- Phase 1
- Development phase
- 1
- Enrollment target
NCT07588581 is a Phase 1 study that is active but no longer recruiting, run by n-Lorem Foundation. The registered enrollment target is 1 participants.
The verdict
NCT07588581, a Phase 1 study, is active but no longer recruiting, sponsored by n-Lorem Foundation.
- ACTIVE NOT RECRUITING
- Registry status
- Phase 1
- Development phase
- 1 participants
- Enrollment target
Study Summary
This research project entails delivery of a personalized antisense oligonucleotide (ASO) drug designed for a single participant with Childhood-Onset Neurodegeneration with Brain Atrophy (CONDBA) due to a heterozygous missense gain-of-function mutation in UBTF
Interventions
- DRUG nL-UBTF-001
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 1 participants |
| Start Date | 2025-02-05 |
| Est. Completion | 2027-02 |
| Phase | Phase 1 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT07588581
The ClinicalTrials.gov registry entry for NCT07588581 describes a study currently listed as active not recruiting, categorized as Phase 1. The registered enrollment target is 1 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is n-Lorem Foundation, which has 12 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 1 intervention - of which nL-UBTF-001 is the first listed.
NCT07588581 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT07588581 about?
NCT07588581 is a clinical study titled "Personalized Antisense Oligonucleotide for A Single Participant With UBTF Gene Mutation". This research project entails delivery of a personalized antisense oligonucleotide (ASO) drug designed for a single participant with Childhood-Onset Neurodegeneration with Brain Atrophy (CONDBA) due to a heterozygous missense gain-of-function mutation in UBTF
What is the current status of trial NCT07588581?
This trial is currently active not recruiting. It is a Phase 1 study. The enrollment target is 1 participants. The study started on 2025-02-05. Estimated completion is 2027-02.
What interventions are being tested in trial NCT07588581?
The interventions under investigation include: nL-UBTF-001 (DRUG).
Who is sponsoring clinical trial NCT07588581?
This trial is sponsored by n-Lorem Foundation, which has 12 total clinical trials registered on ClinicalTrials.gov.
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