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NCT07236606 · ClinicalTrials.gov registry record · Phase 3

RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)

A Phase 3 study, sponsored by REGENXBIO.

Active
Registry status
Phase 3
Development phase
2
Enrollment target

NCT07236606: Active Phase 3 study, sponsored by REGENXBIO.

NCT07236606 is a Phase 3 study that is active but no longer recruiting, run by REGENXBIO. The registered enrollment target is 2 participants, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (100% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT07236606, a Phase 3 study, is active but no longer recruiting, sponsored by REGENXBIO.

ACTIVE NOT RECRUITING
Registry status
Phase 3
Development phase
2 participants
Enrollment target

Study Summary

RGX-121 is a gene therapy which is intended to deliver a functional copy of the iduronate-2-sulfatase gene (IDS) to the central nervous system. This study is a safety, efficacy, and pharmacodynamic dose ranging study to determine whether RGX-121 is safe, effective and well-tolerated by patients with MPS II (Hunter Syndrome)

Primary Outcome

To evaluate the effect of RGX-121 on the neurodevelopmental function as measured by the Bayley Scales of Infant and Toddler Development, 3rd Edition (BSID-III).

Interventions

  • GENETIC RGX-121-3102

Trial Details

FieldValue
Enrollment Target 2 participants
Start Date 2025-11-25
Est. Completion 2031-05-30
Phase Phase 3
REGENXBIO

9 total trials

What the registry record for NCT07236606 still lists

NCT07236606 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 2 participants, a relatively small participant target, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (100% lower).

The record links to 0 conditions, and to 1 intervention - of which RGX-121-3102 is the first listed.

NCT07236606 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT07236606 about?

NCT07236606 is a clinical study titled "RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)". RGX-121 is a gene therapy which is intended to deliver a functional copy of the iduronate-2-sulfatase gene (IDS) to the central nervous system. This study is a safety, efficacy, and pharmacodynamic dose ranging study to determine whether RGX-121 is safe, effective and well-tolerated by patients with...

What is the current status of trial NCT07236606?

This trial is currently active not recruiting. It is a Phase 3 study. The enrollment target is 2 participants. The study started on 2025-11-25. Estimated completion is 2031-05-30.

What interventions are being tested in trial NCT07236606?

The interventions under investigation include: RGX-121-3102 (GENETIC).

Who is sponsoring clinical trial NCT07236606?

This trial is sponsored by REGENXBIO, which has 9 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT07236606's enrollment target sits among peer trials

2 2000th of 2000 the lowest of 2,000 other Phase 3 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 3 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT07236606, the US trial registry maintained by the National Library of Medicine. NCT07236606 (small enrollment · none site footprint · active not recruiting) retrieved and formatted by PlainTrial, see methodology.