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NCT06376162 · ClinicalTrials.gov registry record · Phase 1

Ziftomenib in Combination With Chemotherapy for Children With Relapsed/Refractory Acute Leukemia

A Phase 1 study of Relapsed/Refractory KMT2A-r Acute Leukemia and Relapsed/Refractory NUP98-r Acute Leukemia, sponsored by PedAL BCU.

Recruiting
Registry status
Phase 1
Development phase
20
Enrollment target
20
Study locations

NCT06376162: Recruiting Phase 1 study of Relapsed/Refractory KMT2A-r Acute Leukemia and Relapsed/Refractory NUP98-r Acute Leukemia, sponsored by PedAL BCU.

NCT06376162 is a Phase 1 study of Relapsed/Refractory KMT2A-r Acute Leukemia and Relapsed/Refractory NUP98-r Acute Leukemia that is actively recruiting participants, run by PedAL BCU. The registered enrollment target is 20 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (67% lower). The trial reports 20 study locations across 17 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT06376162, a Phase 1 study of Relapsed/Refractory KMT2A-r Acute Leukemia and Relapsed/Refractory NUP98-r Acute Leukemia, is actively recruiting participants, sponsored by PedAL BCU.

RECRUITING
Registry status
Phase 1
Development phase
20 participants
Enrollment target
20
Study locations

Study Summary

The primary objective of the study is to determine the recommended phase 2 dose (RP2D) of ziftomenib in combination with chemotherapy (FLA) in children with relapsed or refractory KMT2A-r, NUP98-r, or NPM1-m acute leukemia based on safety and pharmacokinetics (PK).

Interventions

  • DRUG Fludarabine
  • DRUG Cytarabine
  • DRUG Ziftomenib

Study Locations (20)

Other

  • Fondazione IRCCS San Gerardo dei Tintori (Ospedale San Gerardo) - Monza
  • Prinses Maxima Centrum Kinderoncologie - Utrecht
  • Hospital Universitari Vall d'Hebrón - Barcelona
  • Hospital Infantil Universitario Niño Jesús - Madrid

California

  • Children's Hospital Los Angeles - Los Angeles

Colorado

  • Children's Hospital Colorado - Aurora

Georgia

  • Children's Healthcare of Atlanta - Atlanta

Illinois

  • Ann & Robert H. Lurie Children's Hospital of Chicago - Chicago

Massachusetts

  • Dana-Farber Cancer Institute - Boston

New York

  • Memorial Sloan Kettering Cancer Center - New York - New York

Ohio

  • Cincinnati Children's Hospital Medical Center - Cincinnati

Trial Details

FieldValue
Enrollment Target 20 participants
Start Date 2025-03-18
Est. Completion 2027-01
Phase Phase 1
PedAL BCU

3 total trials

What NCT06376162 shows while recruiting

NCT06376162 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 20 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (67% lower).

The record links to 3 conditions, with Relapsed/Refractory KMT2A-r Acute Leukemia appearing as the primary indexed condition, and to 3 interventions - of which Fludarabine is the first listed.

NCT06376162 names 20 study sites across 17 states, led by Other, California, Colorado.

Frequently Asked Questions

What is clinical trial NCT06376162 about?

NCT06376162 is a clinical study titled "Ziftomenib in Combination With Chemotherapy for Children With Relapsed/Refractory Acute Leukemia". The primary objective of the study is to determine the recommended phase 2 dose (RP2D) of ziftomenib in combination with chemotherapy (FLA) in children with relapsed or refractory KMT2A-r, NUP98-r, or NPM1-m acute leukemia based on safety and pharmacokinetics (PK).

What is the current status of trial NCT06376162?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 20 participants. The study started on 2025-03-18. Estimated completion is 2027-01.

What conditions does trial NCT06376162 study?

This clinical trial studies the following conditions: Relapsed/Refractory KMT2A-r Acute Leukemia, Relapsed/Refractory NUP98-r Acute Leukemia, Relapsed/Refractory NPM1-m Acute Leukemia.

What interventions are being tested in trial NCT06376162?

The interventions under investigation include: Fludarabine (DRUG), Cytarabine (DRUG), Ziftomenib (DRUG).

Who is sponsoring clinical trial NCT06376162?

This trial is sponsored by PedAL BCU, which has 3 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT06376162 being conducted?

This trial has 20 study locations across California, Colorado, Georgia, Illinois, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

How this trial's enrollment target compares

Where NCT06376162's enrollment target sits among peer trials

20 1629th of 2000 higher than 285 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT06376162, the US trial registry maintained by the National Library of Medicine. NCT06376162 (small enrollment · wide site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.