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NCT06374719 · ClinicalTrials.gov registry record

WiTNNess - TNNT1 Myopathy Natural History Study

A clinical trial of Myopathy and TNNT1-associated Myopathy, sponsored by Clinic for Special Children.

Recruiting
Registry status
40
Enrollment target
1
Study location

NCT06374719: Recruiting study of Myopathy and TNNT1-associated Myopathy, sponsored by Clinic for Special Children.

NCT06374719 is a study of Myopathy and TNNT1-associated Myopathy that is actively recruiting participants, run by Clinic for Special Children. The registered enrollment target is 40 participants, roughly in line with the 41-participant average among 3 other Myopathy trials with a reported enrollment target. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT06374719, a study of Myopathy and TNNT1-associated Myopathy, is actively recruiting participants, sponsored by Clinic for Special Children.

RECRUITING
Registry status
40 participants
Enrollment target
1
Study location

Study Summary

WiTNNess is designed to accurately document the natural course and variation of muscle disease caused by pathogenic changes of the TNNT1 gene. The primary aim of the study is to specify meaningful outcome measures for future clinical trials. WiTNNess is open to children and adults worldwide. Participants can choose to include their information once (cross-sectional cohort) or every few months (prospective cohort).

Primary Outcome

The primary outcome is time until death or permanent ventilatory support, defined as any invasive (e.g., tracheostomy) or non-invasive (e.g., bilevel positive airway pressure) mechanical ventilatory assistance for ≥16 hours daily during ≥14 consecutive days in the absence of a reversible clinical state.

Study Locations (1)

Pennsylvania

  • Clinic for Special Children - Gordonville

Trial Details

FieldValue
Enrollment Target 40 participants
Start Date 2018-09-23
Est. Completion 2027-06-01
Clinic for Special Children

2 total trials

What NCT06374719 shows while recruiting

NCT06374719 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 40 participants, a relatively small participant target, roughly in line with the 41-participant average among 3 other Myopathy trials with a reported enrollment target.

The record links to 10 conditions, with Myopathy appearing as the primary indexed condition, and to 0 interventions.

NCT06374719 reports a single indexed study location in Pennsylvania.

Frequently Asked Questions

What is clinical trial NCT06374719 about?

NCT06374719 is a clinical study titled "WiTNNess - TNNT1 Myopathy Natural History Study". WiTNNess is designed to accurately document the natural course and variation of muscle disease caused by pathogenic changes of the TNNT1 gene. The primary aim of the study is to specify meaningful outcome measures for future clinical trials. WiTNNess is open to children and adults worldwide. Partici...

What is the current status of trial NCT06374719?

This trial is currently recruiting. The enrollment target is 40 participants. The study started on 2018-09-23. Estimated completion is 2027-06-01.

What conditions does trial NCT06374719 study?

This clinical trial studies the following conditions: Myopathy, TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy, Myopathies, Nemaline, Myopathy, Rod.

Who is sponsoring clinical trial NCT06374719?

This trial is sponsored by Clinic for Special Children, which has 2 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT06374719 being conducted?

This trial has 1 study location across Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Source: ClinicalTrials.gov NCT06374719, the US trial registry maintained by the National Library of Medicine. NCT06374719 (small enrollment · single site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.