Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.
NCT06214507 · ClinicalTrials.gov registry record
Danon Disease Natural History Study
A clinical trial of Danon Disease, sponsored by Rocket Pharmaceuticals.
- Recruiting
- Registry status
- 60
- Enrollment target
- 13
- Study locations
NCT06214507: Recruiting study of Danon Disease, sponsored by Rocket Pharmaceuticals.
NCT06214507 is a study of Danon Disease that is actively recruiting participants, run by Rocket Pharmaceuticals. The registered enrollment target is 60 participants. The trial reports 13 study locations across 10 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT06214507, a study of Danon Disease, is actively recruiting participants, sponsored by Rocket Pharmaceuticals.
- RECRUITING
- Registry status
- 60 participants
- Enrollment target
- 13
- Study locations
Study Summary
The goal of this international observational study is to learn about the natural history of Danon disease in male patients (≥8 years of age) and female patients (8 to 50 years of age).
Primary Outcome
Evaluation of change over duration of follow up
Conditions Studied
Interventions
- OTHER No intervention
Study Locations (13)
Other
- German Heart Center Munich - München
- Sheba Medical Center - Ramat Gan
- Azienda Ospedaliero Universitaria - Florence
- University College London - Great Ormond Street Institute of Child Health - London
Arizona
- Phoenix Children's Hospital - Phoenix
California
- University of California, San Diego - La Jolla
Colorado
- Children's Hospital Colorado - Aurora
Florida
- University of Florida College of Medicine - Gainesville
Michigan
- University of Michigan - Ann Arbor
Missouri
- Washington University - St Louis
New York
- Columbia University Medical Center/New York Presbyterian - New York
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 60 participants |
| Start Date | 2023-12-20 |
| Est. Completion | 2030-03 |
What NCT06214507 shows while recruiting
NCT06214507 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 60 participants, a relatively small participant target.
The record links to 1 condition, with Danon Disease appearing as the primary indexed condition, and to 1 intervention - of which No intervention is the first listed.
NCT06214507 lists 13 locations in 10 states (Other, Arizona, California).
Frequently Asked Questions
What is clinical trial NCT06214507 about?
NCT06214507 is a clinical study titled "Danon Disease Natural History Study". The goal of this international observational study is to learn about the natural history of Danon disease in male patients (≥8 years of age) and female patients (8 to 50 years of age).
What is the current status of trial NCT06214507?
This trial is currently recruiting. The enrollment target is 60 participants. The study started on 2023-12-20. Estimated completion is 2030-03.
What conditions does trial NCT06214507 study?
This clinical trial studies the following conditions: Danon Disease.
What interventions are being tested in trial NCT06214507?
The interventions under investigation include: No intervention (OTHER).
Who is sponsoring clinical trial NCT06214507?
This trial is sponsored by Rocket Pharmaceuticals, which has 10 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT06214507 being conducted?
This trial has 13 study locations across Arizona, California, Colorado, Florida, Michigan. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
Learn More About Clinical Trials
Similar trials for Danon Disease
Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.
Nationwide trials with similar profiles
Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.
Similar enrollment target
- NCT00576069 · 60 participants
Mechanism(s)of Airflow Limitation in Moderate-severe Persistent Asthma
- NCT01297400 · 60 participants · Phase 2
Phase 2 Pilot Study of the Safety and Efficacy of Topical MW-III in Thermal Burns
- NCT01734122 · 60 participants
Stereotactic Radiosurgery for Essential Tremor and Parkinsonian Tremor
- NCT01804634 · 60 participants · Phase 2
Reduced Intensity Haploidentical BMT for High Risk Solid Tumors
Similar registry start date
- NCT05962346 · started 2026-12 · NA
Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia
- NCT07125183 · started 2026-12 · Phase 2
Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma
- NCT07292298 · started 2026-11 · Phase 2
Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates
- NCT04263285 · started 2026-10 · NA
Treatment of Depression Post-SCI