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NCT06078553 · ClinicalTrials.gov registry record
A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4
A clinical trial of Congenital Myasthenic Syndrome, sponsored by argenx.
- Recruiting
- Registry status
- 100
- Enrollment target
- 19
- Study locations
NCT06078553 is a study of Congenital Myasthenic Syndrome that is actively recruiting participants, run by argenx. The registered enrollment target is 100 participants. The trial reports 19 study locations across 3 states.
The verdict
NCT06078553, a study of Congenital Myasthenic Syndrome, is actively recruiting participants, sponsored by argenx.
- RECRUITING
- Registry status
- 100 participants
- Enrollment target
- 19
- Study locations
Study Summary
Participants will attend up to 4 study visits to collect clinical assessments. The assessments will evaluate participants' symptoms and quality of life to understand disease activity in patients with CMS due to mutations in DOK7, MUSK, AGRN, or LRP4. More information can be found here: https://clinicaltrials.argenx.com/cms
Conditions Studied
Study Locations (19)
Other
- Medical University of Vienna - Vienna
- The Ottawa Hospital - Civic Campus - Ottawa
- CHU Bordeaux - Groupe Hospitalier Pellegrin - Neurology - Bordeaux
- Hospices Civils de Lyon (HCL) - Hopital Pierre Wertheimer - Neurology - Bron
- CHU Lille Hopital Salengro - Neurology - Lille
- CHU Timone - Marseille
- Assistance Publique Hopitaux de Paris - Hopital Pitie-Salpetriere - Paris
- Universitaetsklinikum Essen (AoR) - Essen
- Fondazione IRCCS Istituto Neurologico Carlo Besta - Milan
- National Hospital Organization Akita Hospital - Neurology - Yurihonjō
- Centrum Medyczne Neurologia Slaska - Neurology - Katowice
- Hospital Sant Joan de Deu - Pediatric Neurology - Esplugues de Llobregat
- Hospital Universitario 12 de Octubre - Madrid
- Hospital Universitari i Politecnic La Fe - Valencia
- Ulster Hospital - Dundonald
- Oxford University Hospitals NHS Foundation Trust - John Radcliffe Hospital - Oxford
Illinois
- Ann and Robert H Lurie Children's Hospital of Chicago - Main Hospital - Chicago
- Hospital Sisters Health System (HSHS) - St Elizabeth's Hospital - O'Fallon
California
- UC Davis Health - UC Davis Health Midtown Ambulatory Care Center - Sacramento
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 100 participants |
| Start Date | 2024-02-13 |
| Est. Completion | 2027-06 |
Interested in This Trial?
Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT06078553
The ClinicalTrials.gov registry entry for NCT06078553 describes a study currently listed as recruiting, categorized as an unspecified phase. The registered enrollment target is 100 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is argenx, which has 49 total studies on file at ClinicalTrials.gov.
The record links to 1 condition, with Congenital Myasthenic Syndrome appearing as the primary indexed condition, and to 0 interventions.
NCT06078553 reports 19 study locations spanning 3 distinct geographic areas - top geographies include Other, Illinois, California.
Frequently Asked Questions
What is clinical trial NCT06078553 about?
NCT06078553 is a clinical study titled "A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4". Participants will attend up to 4 study visits to collect clinical assessments. The assessments will evaluate participants' symptoms and quality of life to understand disease activity in patients with CMS due to mutations in DOK7, MUSK, AGRN, or LRP4. More information can be found here: https://clin...
What is the current status of trial NCT06078553?
This trial is currently recruiting. The enrollment target is 100 participants. The study started on 2024-02-13. Estimated completion is 2027-06.
What conditions does trial NCT06078553 study?
This clinical trial studies the following conditions: Congenital Myasthenic Syndrome.
Who is sponsoring clinical trial NCT06078553?
This trial is sponsored by argenx, which has 49 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT06078553 being conducted?
This trial has 19 study locations across California, Illinois. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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