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NCT05932914 · ClinicalTrials.gov registry record

Liver Biopsy Following Gene Therapy For Hemophilia

A clinical trial, sponsored by St. Jude Children's Research Hospital.

Not yet
Registry status
8
Enrollment target

NCT05932914: Clinical Trial study, sponsored by St. Jude Children's Research Hospital.

NCT05932914 is a clinical trial that has not yet begun recruiting, run by St. Jude Children's Research Hospital. The registered enrollment target is 8 participants. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT05932914 has not yet begun recruiting, sponsored by St. Jude Children's Research Hospital.

NOT YET RECRUITING
Registry status
8 participants
Enrollment target

Study Summary

This observational study will obtain liver biopsy samples and evaluate the long-term effect of adeno-associated virus (AAV)-mediated gene therapy on the liver tissue in adult patients with hemophilia A or hemophilia B who have previously been treated with a factor VIII or factor IX gene-containing AAV-vector for liver-targeted gene transfer. Participants are from a cohort of patients treated with AAV-mediated gene transfer and at least 6 months after vector infusion.

Primary Outcome

Fluorescence in situ hybridization (FISH)

Interventions

  • PROCEDURE Liver Biopsy

Trial Details

FieldValue
Enrollment Target 8 participants
Start Date 2026-07
Est. Completion 2030-01

What is known before NCT05932914 opens enrollment

NCT05932914 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 8 participants, a relatively small participant target.

The record links to 0 conditions, and to 1 intervention - of which Liver Biopsy is the first listed.

NCT05932914 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT05932914 about?

NCT05932914 is a clinical study titled "Liver Biopsy Following Gene Therapy For Hemophilia". This observational study will obtain liver biopsy samples and evaluate the long-term effect of adeno-associated virus (AAV)-mediated gene therapy on the liver tissue in adult patients with hemophilia A or hemophilia B who have previously been treated with a factor VIII or factor IX gene-containing A...

What is the current status of trial NCT05932914?

This trial is currently not yet recruiting. The enrollment target is 8 participants. The study started on 2026-07. Estimated completion is 2030-01.

What interventions are being tested in trial NCT05932914?

The interventions under investigation include: Liver Biopsy (PROCEDURE).

Who is sponsoring clinical trial NCT05932914?

This trial is sponsored by St. Jude Children's Research Hospital, which has 410 total clinical trials registered on ClinicalTrials.gov.

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Source: ClinicalTrials.gov NCT05932914, the US trial registry maintained by the National Library of Medicine. NCT05932914 (small enrollment · none site footprint · not yet recruiting) retrieved and formatted by PlainTrial, see methodology.