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NCT05705674 · ClinicalTrials.gov registry record

The Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)

A clinical trial of Sanfilippo Syndrome and MPS3, sponsored by Lysosomal and Rare Disorders Research and Treatment Center.

Recruiting
Registry status
6
Enrollment target
1
Study location

NCT05705674: Recruiting study of Sanfilippo Syndrome and MPS3, sponsored by Lysosomal and Rare Disorders Research and Treatment Center.

NCT05705674 is a study of Sanfilippo Syndrome and MPS3 that is actively recruiting participants, run by Lysosomal and Rare Disorders Research and Treatment Center. The registered enrollment target is 6 participants. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT05705674, a study of Sanfilippo Syndrome and MPS3, is actively recruiting participants, sponsored by Lysosomal and Rare Disorders Research and Treatment Center.

RECRUITING
Registry status
6 participants
Enrollment target
1
Study location

Study Summary

The natural history study of patients with Sanfilippo disease(s) (MPS3)

Conditions Studied

Study Locations (1)

Virginia

  • LDRTC - Fairfax

Trial Details

FieldValue
Enrollment Target 6 participants
Start Date 2023-05-01
Est. Completion 2024-12

What NCT05705674 shows while recruiting

NCT05705674 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 6 participants, a relatively small participant target.

The record links to 2 conditions, with Sanfilippo Syndrome appearing as the primary indexed condition, and to 0 interventions.

NCT05705674 reports a single indexed study location in Virginia.

Frequently Asked Questions

What is clinical trial NCT05705674 about?

NCT05705674 is a clinical study titled "The Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)". The natural history study of patients with Sanfilippo disease(s) (MPS3)

What is the current status of trial NCT05705674?

This trial is currently recruiting. The enrollment target is 6 participants. The study started on 2023-05-01. Estimated completion is 2024-12.

What conditions does trial NCT05705674 study?

This clinical trial studies the following conditions: Sanfilippo Syndrome, MPS3.

Who is sponsoring clinical trial NCT05705674?

This trial is sponsored by Lysosomal and Rare Disorders Research and Treatment Center, which has 1 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05705674 being conducted?

This trial has 1 study location across Virginia. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Source: ClinicalTrials.gov NCT05705674, the US trial registry maintained by the National Library of Medicine. NCT05705674 (small enrollment · single site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.