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NCT05648851 · ClinicalTrials.gov registry record
A Natural History Study of Sanfilippo Syndrome Type D
A clinical trial, sponsored by Phoenix Nest.
- Completed
- Registry status
- 10
- Enrollment target
NCT05648851 is a clinical trial that has completed, run by Phoenix Nest. The registered enrollment target is 10 participants.
The verdict
NCT05648851 has completed, sponsored by Phoenix Nest.
- COMPLETED
- Registry status
- 10 participants
- Enrollment target
Study Summary
Sanfilippo syndrome type D is a ultra rare syndrome with limited available natural history data. This study is planned to document, through retrospective and prospective data collection, syndrome progression in children and young adults with Sanfilippo syndrome type D. The results from this study may inform future clinical studies in targeted therapies for patients with Sanfilippo syndrome type D and may serve as an external control since there are very few patients with Sanfilippo syndrome type D.
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 10 participants |
| Start Date | 2023-01-22 |
| Est. Completion | 2024-11-01 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT05648851
The ClinicalTrials.gov registry entry for NCT05648851 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 10 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Phoenix Nest, which has 2 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 0 interventions.
NCT05648851 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT05648851 about?
NCT05648851 is a clinical study titled "A Natural History Study of Sanfilippo Syndrome Type D". Sanfilippo syndrome type D is a ultra rare syndrome with limited available natural history data. This study is planned to document, through retrospective and prospective data collection, syndrome progression in children and young adults with Sanfilippo syndrome type D. The results from this study ma...
What is the current status of trial NCT05648851?
This trial is currently completed. The enrollment target is 10 participants. The study started on 2023-01-22. Estimated completion is 2024-11-01.
Who is sponsoring clinical trial NCT05648851?
This trial is sponsored by Phoenix Nest, which has 2 total clinical trials registered on ClinicalTrials.gov.
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