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NCT05241444 · ClinicalTrials.gov registry record · Phase 1

CD4^LVFOXP3 in Participants With IPEX

A Phase 1 study of IPEX, sponsored by Bacchetta, Rosa, MD.

Recruiting
Registry status
Phase 1
Development phase
30
Enrollment target
1
Study location

NCT05241444: Recruiting Phase 1 study of IPEX, sponsored by Bacchetta, Rosa, MD.

NCT05241444 is a Phase 1 study of IPEX that is actively recruiting participants, run by Bacchetta, Rosa, MD. The registered enrollment target is 30 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (50% lower). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT05241444, a Phase 1 study of IPEX, is actively recruiting participants, sponsored by Bacchetta, Rosa, MD.

RECRUITING
Registry status
Phase 1
Development phase
30 participants
Enrollment target
1
Study location

Study Summary

This first-in-human, Phase 1 clinical trial will test the feasibility of the manufacturing and the safety of the administration of CD4\^LVFOXP3 in up to 30 evaluable human participants with IPEX and evaluate the impact of the CD4\^LVFOXP3 infusion on the disease.

Primary Outcome

No more than two products fail the target cell dose and established release criteria.

Conditions Studied

Interventions

  • BIOLOGICAL CD4^LVFOXP3

Study Locations (1)

California

  • Lucile Packard Children's Hospital - Palo Alto

Trial Details

FieldValue
Enrollment Target 30 participants
Start Date 2022-03-22
Est. Completion 2037-02
Phase Phase 1
Bacchetta, Rosa, MD

1 total trials

What NCT05241444 shows while recruiting

NCT05241444 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 30 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (50% lower).

The record links to 1 condition, with IPEX appearing as the primary indexed condition, and to 1 intervention - of which CD4^LVFOXP3 is the first listed.

NCT05241444 reports a single indexed study location in California.

Frequently Asked Questions

What is clinical trial NCT05241444 about?

NCT05241444 is a clinical study titled "CD4^LVFOXP3 in Participants With IPEX". This first-in-human, Phase 1 clinical trial will test the feasibility of the manufacturing and the safety of the administration of CD4\^LVFOXP3 in up to 30 evaluable human participants with IPEX and evaluate the impact of the CD4\^LVFOXP3 infusion on the disease.

What is the current status of trial NCT05241444?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 30 participants. The study started on 2022-03-22. Estimated completion is 2037-02.

What conditions does trial NCT05241444 study?

This clinical trial studies the following conditions: IPEX.

What interventions are being tested in trial NCT05241444?

The interventions under investigation include: CD4^LVFOXP3 (BIOLOGICAL).

Who is sponsoring clinical trial NCT05241444?

This trial is sponsored by Bacchetta, Rosa, MD, which has 1 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05241444 being conducted?

This trial has 1 study location across California. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

How this trial's enrollment target compares

Where NCT05241444's enrollment target sits among peer trials

30 1333rd of 2000 higher than 561 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT05241444, the US trial registry maintained by the National Library of Medicine. NCT05241444 (small enrollment · single site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.